AAV-Mediated Delivery of Plakophilin-2a Arrests Progression of Arrhythmogenic Right Ventricular Cardiomyopathy in Murine Hearts: Preclinical Evidence Supporting Gene Therapy in Humans
AAV介导的Plakophilin-2a递送可阻止小鼠心脏中致心律失常性右室心肌病的进展:支持人类基因治疗的临床前证据
期刊:Circulation-Genomic and Precision Medicine
影响因子:5.5
doi:10.1161/CIRCGEN.123.004305
van Opbergen, Chantal J M; Narayanan, Bitha; Sacramento, Chester B; Stiles, Katie M; Mishra, Vartika; Frenk, Esther; Ricks, David; Chen, Grace; Zhang, Mingliang; Yarabe, Paul; Schwartz, Jonathan; Delmar, Mario; Herzog, Chris D; Cerrone, Marina