日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Waning efficacy in a long-term AAV-mediated gene therapy study in the murine model of Krabbe disease

针对克拉伯病小鼠模型的长期 AAV 介导基因治疗研究的疗效逐渐减弱

Gregory J Heller, Michael S Marshall, Yazan Issa, Jeffrey N Marshall, Duc Nguyen, Emily Rue, Koralege C Pathmasiri, Miriam S Domowicz, Richard B van Breemen, Leon M Tai, Stephanie M Cologna, Stephen J Crocker, Maria I Givogri, Mark S Sands, Ernesto R Bongarzone

Barriers of Occupational Safety Implementation in Infrastructure Projects: Gaza Strip Case

基础设施项目职业安全实施的障碍:以加沙地带为例

Abu Aisheh, Yazan Issa; Tayeh, Bassam A; Alaloul, Wesam Salah; Jouda, Amro Fareed

AAV-Mediated GALC Gene Therapy Rescues Alpha-Synucleinopathy in the Spinal Cord of a Leukodystrophic Lysosomal Storage Disease Mouse Model

AAV 介导的 GALC 基因疗法挽救了白质营养不良性溶酶体贮积症小鼠模型脊髓中的 α-突触核蛋白病

Michael S Marshall, Yazan Issa, Gregory Heller, Duc Nguyen, Ernesto R Bongarzone

Long-Term Improvement of Neurological Signs and Metabolic Dysfunction in a Mouse Model of Krabbe's Disease after Global Gene Therapy

克拉伯氏病小鼠模型接受整体基因治疗后神经系统症状和代谢功能障碍得到长期改善

Michael S Marshall, Yazan Issa, Benas Jakubauskas, Monika Stoskute, Vince Elackattu, Jeffrey N Marshall, Wil Bogue, Duc Nguyen, Zane Hauck, Emily Rue, Subha Karumuthil-Melethil, Violeta Zaric, Maarten Bosland, Richard B van Breemen, Maria I Givogri, Steven J Gray, Stephen J Crocker, Ernesto R Bongar

α-Synuclein interacts directly but reversibly with psychosine: implications for α-synucleinopathies

α-突触核蛋白与精神氨酸直接但可逆地相互作用:对 α-突触核蛋白病的影响

Hazem Abdelkarim, Michael S Marshall, Giuseppe Scesa, Rachael A Smith, Emily Rue, Jeffrey Marshall, Vince Elackattu, Monika Stoskute, Yazan Issa, Marta Santos, Duc Nguyen, Zane Hauck, Richard van Breemen, Maria S Celej, Vadim Gaponenko, Ernesto R Bongarzone