日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Author Correction: In vivo base editing extends lifespan of a humanized mouse model of prion disease

作者更正:体内碱基编辑延长了朊病毒病人源化小鼠模型的寿命

An, Meirui; Davis, Jessie R; Levy, Jonathan M; Serack, Fiona E; Harvey, John W; Brauer, Pamela P; Pirtle, Catherine P; Berríos, Kiara N; Newby, Gregory A; Yeh, Wei-Hsi; Kamath, Nikita; Mortberg, Meredith; Lian, Yuan; Howard, Michael; DeSouza-Lenz, Kendrick; Guzman, Kenia; Thai, Aaron; Graffam, Samantha; Laversenne, Vanessa; Coffey, Alissa A; Frei, Jeannine; Pierce, Sarah E; Safar, Jiri G; Deverman, Benjamin E; Minikel, Eric Vallabh; Vallabh, Sonia M; Liu, David R

In vivo base editing extends lifespan of a humanized mouse model of prion disease.

体内碱基编辑延长了朊病毒疾病人源化小鼠模型的寿命

An Meirui, Davis Jessie R, Levy Jonathan M, Serack Fiona E, Harvey John W, Brauer Pamela P, Pirtle Catherine P, Berríos Kiara N, Newby Gregory A, Yeh Wei-Hsi, Kamath Nikita, Mortberg Meredith, Lian Yuan, Howard Michael, DeSouza-Lenz Kendrick, Guzman Kenia, Thai Aaron, Graffam Samantha, Laversenne Vanessa, Coffey Alissa A, Frei Jeannine, Pierce Sarah E, Safar Jiri G, Deverman Benjamin E, Minikel Eric Vallabh, Vallabh Sonia M, Liu David R

Generating experimentally unrelated target molecule-binding highly functionalized nucleic-acid polymers using machine learning

利用机器学习生成与实验无关的靶分子结合的高功能化核酸聚合物

Chen, Jonathan C; Chen, Jonathan P; Shen, Max W; Wornow, Michael; Bae, Minwoo; Yeh, Wei-Hsi; Hsu, Alvin; Liu, David R

In vivo base editing restores sensory transduction and transiently improves auditory function in a mouse model of recessive deafness

体内碱基编辑可恢复隐性耳聋小鼠模型的听觉转导并暂时改善听觉功能

Yeh, Wei-Hsi; Shubina-Oleinik, Olga; Levy, Jonathan M; Pan, Bifeng; Newby, Gregory A; Wornow, Michael; Burt, Rachel; Chen, Jonathan C; Holt, Jeffrey R; Liu, David R

Continuous evolution of base editors with expanded target compatibility and improved activity.

碱基编辑器不断发展,具有更广泛的靶标兼容性和更高的活性

Thuronyi B W, Koblan Luke W, Levy Jonathan M, Yeh Wei-Hsi, Zheng Christine, Newby Gregory A, Wilson Christopher, Bhaumik Mantu, Shubina-Oleinik Olga, Holt Jeffrey R, Liu David R