Preclinical evaluation of AGT mRNA replacement therapy for primary hyperoxaluria type I disease
AGT mRNA替代疗法治疗原发性高草酸尿症I型疾病的临床前评估
期刊:Science Advances
影响因子:11.7
doi:10.1126/sciadv.adt9694.
Taihua Yang,Jiahao Ge,Lei Huang,Xinye Zhu,Dexin Zhang,Siyuan Tang,Jie Zhao,Yinhe Ma,Mei Long,Xiaochen Bo,Jie Li,Yiqing Zhang,Qinggong Yuan,Amar Deep Sharma,Michael Ott,Hongquan Geng,Yicheng Zhao,Liang Zhang,Haifa Shen,Hangwen Li,Dali Li,Ping Wan,Qiang Xia