日期 影响因子
日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:
–

Phase 1/2 trial of brogidirsen: Dual-targeting antisense oligonucleotides for exon 44 skipping in Duchenne muscular dystrophy

brogidirsen 的 1/2 期试验：用于杜氏肌营养不良症外显子 44 跳跃的双靶点反义寡核苷酸

期刊:Cell Reports Medicine
影响因子:11.7
doi:10.1016/j.xcrm.2024.101901
Hirofumi Komaki,Eri Takeshita,Katsuhiko Kunitake,Takami Ishizuka,Yuko Shimizu-Motohashi,Akihiko Ishiyama,Masayuki Sasaki,Chihiro Yonee,Shinsuke Maruyama,Eisuke Hida,Yoshitsugu Aoki
发表日期：2025
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Intrathecal Baclofen Therapy Improves Refractory Status Dystonicus in Neuro-hepatic Wilson's Disease: A Case Report

鞘内注射巴氯芬治疗改善神经肝性威尔逊病难治性肌张力障碍：病例报告

期刊:
影响因子:
doi:10.2176/jns-nmc.2024-0234
Yamanaka, Sae; Hanada, Tomoko; Higashi, Takuichiro; Matsunaga, Manaka; Yonee, Chihiro; Maruyama, Shinsuke; Hanaya, Ryosuke
发表日期：2025
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Systemic administration of the antisense oligonucleotide NS-089/NCNP-02 for skipping of exon 44 in patients with Duchenne muscular dystrophy: Study protocol for a phase I/II clinical trial

系统性应用反义寡核苷酸NS-089/NCNP-02治疗杜氏肌营养不良症患者，以跳跃外显子44：一项I/II期临床试验的研究方案

期刊:Neuropsychopharmacology Reports
影响因子:1.5
doi:10.1002/npr2.12335
Ishizuka, Takami; Komaki, Hirofumi; Asahina, Yasuko; Nakamura, Harumasa; Motohashi, Norio; Takeshita, Eri; Shimizu-Motohashi, Yuko; Ishiyama, Akihiko; Yonee, Chihiro; Maruyama, Shinsuke; Hida, Eisuke; Aoki, Yoshitsugu
发表日期：2023
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Exploratory evaluation of an eye-tracking system in patients with advanced spinal muscular atrophy type I receiving nusinersen

对接受诺西那生治疗的晚期I型脊髓性肌萎缩症患者的眼动追踪系统进行探索性评估

期刊:Frontiers in Neurology
影响因子:2.8
doi:10.3389/fneur.2022.918255
Yae, Yukako; Yuge, Kotaro; Maeda, Toshiyuki; Ichinose, Fumio; Matsuo, Muneaki; Kobayashi, Osamu; Okanari, Kazuo; Baba, Yusei; Yonee, Chihiro; Maruyama, Shinsuke; Shibata, Minoru; Fujii, Tatsuya; Chinen, Madoka; Yamashita, Yushiro
神经科学
肌萎缩症
发表日期：2022
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