A Systemically Administered Unconjugated Antisense Oligonucleotide Targeting DUX4 Improves Muscular Injury and Motor Function in FSHD Model Mice
全身给药靶向 DUX4 的非共轭反义寡核苷酸可改善 FSHD 模型小鼠的肌肉损伤和运动功能
期刊:Biomedicines
影响因子:3.9
doi:10.3390/biomedicines11092339
Tetsuhiro Kakimoto, Akira Ogasawara, Kiyoshi Ishikawa, Takashi Kurita, Kumiko Yoshida, Shuichi Harada, Taeko Nonaka, Yoshimi Inoue, Keiko Uchida, Takashi Tateoka, Tetsuya Ohta, Shinji Kumagai, Takashi Sasaki, Hajime Aihara
