Administration of a barcoded AAV capsid library to the putamen of non-human primates identifies variants with efficient retrograde transport.
将带有条形码的 AAV 衣壳文库施用于非人灵长类动物的壳核,以鉴定具有高效逆行运输能力的变体。
期刊:Molecular Therapy
影响因子:12
doi:10.1016/j.ymthe.2025.12.009
Dzhashiashvili Yulia, McBride Jodi L, Fabyanic Emily, Huang Xin, Kelly Brian M, Walton-Gibbs Greglynn D, Vemireddi Vimala, Wicks Joan, Nayal Mohamad, Hippen Ariel A, Yu Zhenming, Raman Pichai, Ramsburg Elizabeth, Davidsson Marcus, Engel Esteban A, Björklund Tomas