An Engineered Intravitreal Injection Retinal-Pigment-Epithelium-Tropic Adeno-Associated Virus Vector Expressing a Bispecific Antibody Binding VEGF-A and ANG-2 Rescues Neovascular Age-Related Macular Degeneration in Animal Models and Patients
一种表达结合 VEGF-A 和 ANG-2 的双特异性抗体的工程化玻璃体内注射视网膜色素上皮嗜性腺相关病毒载体,可挽救动物模型和患者的新生血管性年龄相关性黄斑变性。
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doi:10.34133/research.0717
Cai, Yuan; Gu, Yonghao; Zhang, Jie; Zhu, Ying; Ma, Zhen; He, Qin; Sun, Yongjia; Yuan, Mengmeng; Li, Xiaojun; Zhu, Kai; Miao, Bolong; Zhao, Jin; Liu, Juan; Tang, Min; Tong, Dali; Feng, Lixia; Ma, Ming; Zhong, Guisheng; Qiu, Zilong; Xue, Tian