日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Seamless Gene Correction in the Human Cystic Fibrosis Transmembrane Conductance Regulator Locus by Vector Replacement and Vector Insertion Events

通过载体置换和载体插入事件实现人类囊性纤维化跨膜传导调节基因座的无缝基因校正

Shingo Suzuki, Keisuke Chosa, Cristina Barillà, Michael Yao, Orsetta Zuffardi, Hirofumi Kai, Tsuyoshi Shuto, Mary Ann Suico, Yuet W Kan, R Geoffrey Sargent, Dieter C Gruenert

TALENs Facilitate Single-step Seamless SDF Correction of F508del CFTR in Airway Epithelial Submucosal Gland Cell-derived CF-iPSCs

TALENs促进气道上皮黏膜下腺细胞来源的CF-iPSCs中F508del CFTR的单步无缝SDF校正

Suzuki, Shingo; Sargent, R Geoffrey; Illek, Beate; Fischer, Horst; Esmaeili-Shandiz, Alaleh; Yezzi, Michael J; Lee, Albert; Yang, Yanu; Kim, Soya; Renz, Peter; Qi, Zhongxia; Yu, Jingwei; Muench, Marcus O; Beyer, Ashley I; Guimarães, Alessander O; Ye, Lin; Chang, Judy; Fine, Eli J; Cradick, Thomas J; Bao, Gang; Rahdar, Meghdad; Porteus, Matthew H; Shuto, Tsuyoshi; Kai, Hirofumi; Kan, Yuet W; Gruenert, Dieter C

Permanent coronary artery occlusion: cardiovascular MR imaging is platform for percutaneous transendocardial delivery and assessment of gene therapy in canine model

永久性冠状动脉闭塞:心血管磁共振成像平台可用于经皮经心内膜基因治疗在犬模型中的应用及评估

Saeed, Maythem; Martin, Alastair; Jacquier, Alexis; Bucknor, Matthew; Saloner, David; Do, Loi; Ursell, Philip; Su, Hua; Kan, Yuet W; Higgins, Charles B