Cell-mediated exon skipping normalizes dystrophin expression and muscle function in a new mouse model of Duchenne Muscular Dystrophy
细胞介导的外显子跳跃使新型杜氏肌营养不良症小鼠模型中的肌营养不良蛋白表达和肌肉功能正常化
期刊:EMBO Molecular Medicine
影响因子:9
doi:10.1038/s44321-024-00031-3
Francesco Galli, Laricia Bragg, Maira Rossi, Daisy Proietti, Laura Perani, Marco Bacigaluppi, Rossana Tonlorenzi, Tendai Sibanda, Miriam Caffarini, Avraneel Talapatra, Sabrina Santoleri, Mirella Meregalli, Beatriz Bano-Otalora, Anne Bigot, Irene Bozzoni, Chiara Bonini, Vincent Mouly, Yvan Torrente,