CTNI-21. PIVOTAL, PHASE 2B RENEU TRIAL OF MIRDAMETINIB IN CHILDREN AND ADULTS WITH NEUROFIBROMATOSIS TYPE 1-ASSOCIATED PLEXIFORM NEUROFIBROMA (NF1-PN): A SPOTLIGHT ON PATIENTS ACHIEVING DEEP RESPONSE
CTNI-21. 针对患有 1 型神经纤维瘤病相关丛状神经纤维瘤 (NF1-PN) 的儿童和成人的 MIRDAMETINIB 关键性 2b 期 RENEU 试验:聚焦获得深度缓解的患者
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doi:10.1016/j.vgie.2023.01.001
Gorrepati, Venkata Subhash; Yang, Dennis; Draganov, Peter V; Marcella, Stephen; Kobic, Emir; Carr, Amy L; Georgiades, Benjamin; Margiotta, Caroline; Ackley, Renee; Roshdy, Danya; Isip, Jacqueline; Minor, Sarah B,; Elchynski, Amanda L; Anderson, William E; Capraro, Gerald A; Polk, Christopher; Marx, Ashley H; Chundi, Vahini; Zaccardelli, Jill; Angle, Timothy; Oriet, Jonathan; Swartwood, Michael J; Boyce, Ross; Daniels, Lindsay M; Juliano, Jonathan J; Gershon, Timothy; Moertel, Christopher; McNall-Knapp, Rene; Shuhaiber, Hans; Weintraub, Lauren; Hajjar, Fouad; Nickerson, Molly; Weber, Michael; Lokku, Armend; Babovic-Vuksanovic, Dusica; Hirbe, Angela