Structural characterization of antibody-responses following Zolgensma treatment for AAV capsid engineering to expand patient cohorts.
对Zolgensma治疗后抗体反应的结构进行表征，以进行AAV衣壳工程改造，从而扩大患者群体
期刊:Nature Communications
影响因子:15.7
doi:10.1038/s41467-025-59088-4
Mietzsch Mario, Hsi Jane, Nelson Austin R, Khandekar Neeta, Huang Ann-Maree, Smith Nicholas Jc, Zachary Jon, Potts Lindsay, Farrar Michelle A, Chipman Paul, Ghanem Mohammad, Alexander Ian E, Logan Grant J, Huiskonen Juha T, McKenna Robert
