日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Muscle MRI quantifies disease progression in amyotrophic lateral sclerosis

肌肉磁共振成像可量化肌萎缩侧索硬化症的疾病进展

Klickovic, Uros; Zampedri, Luca; Zafeiropoulos, Nick; Ziff, Oliver J; Sinclair, Christopher Dj; Wastling, Stephen; Dudziec, Magdalena; Allen, Jodie; Trimmel, Karin; Howard, Robin S; Malaspina, Andrea; Sharma, Nikhil; Sidle, Katie Cl; Shah, Sachit; Nasel, Christian; Yousry, Tarek A; Greensmith, Linda; Morrow, Jasper M; Thornton, John S; Fratta, Pietro

TDP-43 pathology induces CD8(+) T cell activation through cryptic epitope recognition.

TDP-43 病理通过隐蔽表位识别诱导 CD8(+) T 细胞活化

Chizari Shahab, Zanovello Matteo, Kong Steven, Saigal Vidur, Brown Anna-Leigh, Turchetti Valentina, Zampedri Luca, Skorupinska Iwona, Minicuci Giacomo Maria, Paron Francesca, Tonin Paola, Marchetto Giulia, Li Ziyi, Colón-Mercado Jennifer M, Dattilo Dario, Barattucci Simone, Gatt Ariana, Qi Andy, Hanna Michael, Ward Michael, Petrucelli Leonard, Romano Maurizio, Vattemi Gaetano, Buratti Emanuele, Malapsina Andrea, Merve Ashirwad, Machado Pedro M, Soraru Gianni, Fratta Pietro, Jiang Ning

Functional Outcome Measures to Optimize Drug Development in Spinal and Bulbar Muscular Atrophy: Results From a Meta-Analysis of the Global SBMA Dataset

功能性结局指标在脊髓延髓肌萎缩症药物研发优化中的应用:全球 SBMA 数据集荟萃分析结果

Huggett, Spencer B; Tebbenkamp, Andrew T N; Rinaldi, Carlo; Jayaseelan, Dipa; Zampedri, Luca; Blasi, Lorenzo; Fortuna, Andrea; Alqahtani, Abdullah; Kokkinis, Angela; Dahlqvist, Julia; Fenu, Silvia; Cavalca, Eleonora; Bertini, Alessandro; Mariotti, Caterina; Grunseich, Christopher; Kawase, Takahiro; Kishimoto, Yoshiyuki; Yamada, Shinichiro; Katsuno, Masahisa; Fratta, Pietro; Conte, Amelia; Sabatelli, Mario; Soraru, Gianni; Vissing, John; Kang, Minsung; Park, Jin-Sung; Pareyson, Davide; Viglietta, Vissia

Protein biomarker signature in patients with spinal and bulbar muscular atrophy

脊髓延髓肌萎缩症患者的蛋白质生物标志物特征

Tebbenkamp, Andrew Tn; Huggett, Spencer B; Lombardi, Vittoria; Zampedri, Luca; AlQahtani, Abdullah; Kokkinis, Angela; Malaspina, Andrea; Rinaldi, Carlo; Grunseich, Christopher; Fratta, Pietro; Viglietta, Vissia

Skeletal muscle MRI differentiates SBMA and ALS and correlates with disease severity

骨骼肌磁共振成像可以区分脊髓延髓肌萎缩症(SBMA)和肌萎缩侧索硬化症(ALS),并且与疾病严重程度相关。

Klickovic, Uros; Zampedri, Luca; Sinclair, Christopher D J; Wastling, Stephen J; Trimmel, Karin; Howard, Robin S; Malaspina, Andrea; Sharma, Nikhil; Sidle, Katie; Emira, Ahmed; Shah, Sachit; Yousry, Tarek A; Hanna, Michael G; Greensmith, Linda; Morrow, Jasper M; Thornton, John S; Fratta, Pietro