RNA interference therapy targeting coagulation factor XI: a first-in-human trial of RBD4059 (vortosiran)
靶向凝血因子XI的RNA干扰疗法:RBD4059(vortosiran)的首次人体试验
期刊:Blood Advances
影响因子:7.1
doi:10.1182/bloodadvances.2025018348
Gabrielsen, Anders; Ueckert, Sebastian; Nilsson, Catarina; Egnell, Ann-Charlotte; Fu, Jing; Wikström, Johannes; Svedlund, Sara; Friend, Richard; Zhang, Hongyan; Liang, Zicai; Gao, Shan; Gan, Li-Ming