Development of a rabbit model for adrenoleukodystrophy: A pilot study on gene therapy using rAAV9
建立肾上腺脑白质营养不良兔模型:一项使用rAAV9进行基因治疗的初步研究
期刊:Molecular Therapy-Nucleic Acids
影响因子:6.5
doi:10.1016/j.omtn.2025.102469
Xiaoya Zhou ,Chui-Yan Ma ,Xiaoxian Zhang ,Xianchuan Xu ,Fuyu Duan ,Meng Kou ,Hongsheng Liu ,Liang Zeng ,Liyan Guo ,Shaoxiang Chen ,Li Chen ,Ziyue Li ,Jie Luo ,Jieying Wu ,Zhejin Li ,Zhanjun Li ,Tingting Sui ,Ping Yuan ,Zhijian Lin ,Hao Chen ,Liangxue Lai ,Qizhou Lian