CRISPR activation for SCN2A-related neurodevelopmental disorders
CRISPR激活治疗SCN2A相关神经发育障碍
期刊:Nature
影响因子:48.5
doi:10.1038/s41586-025-09522-w
Tamura, Serena; Nelson, Andrew D; Spratt, Perry W E; Hamada, Elizabeth C; Zhou, Xujia; Kyoung, Henry; Li, Zizheng; Arnould, Coline; Barskyi, Vladyslav; Krupkin, Beniamin; Young, Kiana; Zhao, Jingjing; Holden, Stephanie S; Sahagun, Atehsa; Keeshen, Caroline M; Lu, Congyi; Ben-Shalom, Roy; Taloma, Sunrae E; Schamiloglu, Selin; Li, Ying C; Min, Lia; Jenkins, Paul M; Pan, Jen Q; Paz, Jeanne T; Sanders, Stephan J; Matharu, Navneet; Ahituv, Nadav; Bender, Kevin J
