Adenine base editing-mediated exon skipping restores dystrophin in humanized Duchenne mouse model
腺嘌呤碱基编辑介导的外显子跳跃在人源化杜氏小鼠模型中恢复肌营养不良蛋白
期刊:Nature Communications
影响因子:14.7
doi:10.1038/s41467-024-50340-x
Jiajia Lin #, Ming Jin #, Dong Yang #, Zhifang Li #, Yu Zhang #, Qingquan Xiao, Yin Wang, Yuyang Yu, Xiumei Zhang, Zhurui Shao, Linyu Shi, Shu Zhang, Wan-Jin Chen, Ning Wang, Shiwen Wu, Hui Yang, Chunlong Xu, Guoling Li