日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

RNA N6-methyladenosine (m6A) regulates cell cycle progression in diffuse midline glioma (DMG) and confers sensitivity to FTO inhibition

RNA N6-甲基腺苷(m6A)调控弥漫性中线胶质瘤(DMG)的细胞周期进程,并赋予其对FTO抑制剂的敏感性。

Ross, Samuel E; Holliday, Holly; Wang, Eyden; Zeraati, Mahdi; Tsoli, Maria; Ziegler, David S; Dinger, Marcel E

A new hope: Clinical advances in targeted therapies for pediatric diffuse midline glioma

新的希望:儿童弥漫性中线胶质瘤靶向治疗的临床进展

Zhu, Joshua; Tsoli, Maria; Bertoldo, Jean; Mueller, Sabine; Ziegler, David S

Author Correction: The type II RAF inhibitor tovorafenib in relapsed/refractory pediatric low-grade glioma: the phase 2 FIREFLY-1 trial

作者更正:II型RAF抑制剂托沃拉非尼治疗复发/难治性儿童低级别胶质瘤:II期FIREFLY-1试验

Kilburn, Lindsay B; Khuong-Quang, Dong-Anh; Hansford, Jordan R; Landi, Daniel; van der Lugt, Jasper; Leary, Sarah E S; Driever, Pablo Hernáiz; Bailey, Simon; Perreault, Sébastien; McCowage, Geoffrey; Waanders, Angela J; Ziegler, David S; Witt, Olaf; Baxter, Patricia A; Kang, Hyoung Jin; Hassall, Timothy E; Han, Jung Woo; Hargrave, Darren; Franson, Andrea T; Yalon Oren, Michal; Toledano, Helen; Larouche, Valérie; Kline, Cassie; Abdelbaki, Mohamed S; Jabado, Nada; Gottardo, Nicholas G; Gerber, Nicolas U; Whipple, Nicholas S; Segal, Devorah; Chi, Susan N; Oren, Liat; Tan, Enrica E K; Mueller, Sabine; Cornelio, Izzy; McLeod, Lisa; Zhao, Xin; Walter, Ashley; Da Costa, Daniel; Manley, Peter; Blackman, Samuel C; Packer, Roger J; Nysom, Karsten

P01.15.A SINGLE NUCLEUS TRANSCRIPTOMICS OF SPINAL EPENDYMOMA TYPES AND SUBTYPES RECOGNIZES INTRATUMORAL HETEROGENEITY

P01.15.脊髓室管膜瘤类型和亚型的单核转录组学识别肿瘤内异质性

Wang, Anqi; Qi, Dianjun; Ma, Yi; Wang, Mozhi; Dong, Haoran; Wang, Chenxin; Zhang, Yingfan; Zhang, Zheyuan; Li, Lingwei; Xu, Jiayi; Yao, Litong; Xu, Yingying; Holliday, Holly; Ehteda, Anahid; Khan, Aaminah; Krug, Brian; Rouaen, Jourdin R C; Jayatilleke, Nisitha; Mayoh, Chelsea; Vittorio, Orazio; Jabado, Nada; Tsoli, Maria; Ziegler, David S; Hack, K; Jauch-Speer, S; Kresbach, C; Thomas, C; Schüller, U

The Super Enhancer-Driven Long Noncoding RNA PRKCQ-AS1 Promotes Neuroblastoma Tumorigenesis by Interacting With MSI2 Protein and Is Targetable by Small Molecule Compounds.

超级增强子驱动的长链非编码RNA PRKCQ-AS1通过与MSI2蛋白相互作用促进神经母细胞瘤的发生,并且可作为小分子化合物的靶点

Mondal Sujanna, Liu Pei Y, Seneviratne Janith, De Weck Antoine, Venkat Pooja, Mayoh Chelsea, Wu Jing, Maag Jesper, Chen Jingwei, Wong Matthew, Bartonicek Nenad, Khoo Poh, Jin Lei, Ludlow Louise E, Ziegler David S, Trahair Toby, Mestdagh Pieter, Cheung Belamy B, Li Jinyan, Dinger Marcel E, Street Ian, Zhang Xu D, Marshall Glenn M, Liu Tao

Radiographic and visual response to the type II RAF inhibitor tovorafenib in children with relapsed/refractory optic pathway glioma in the FIREFLY-1 trial

FIREFLY-1试验中,复发/难治性视路胶质瘤患儿对II型RAF抑制剂托沃拉非尼的放射学和视觉反应

Nysom, Karsten; Kilburn, Lindsay B; Leary, Sarah E S; Landi, Daniel B; de Vos-Kerkhof, Evelien; Perreault, Sébastien; Witt, Olaf; Ziegler, David S; Hernáiz Driever, Pablo; Franson, Andrea T; Baxter, Patricia A; Whipple, Nicholas S; Kline, Cassie; Segal, Devorah; Jabado, Nada; Bailey, Simon; McCowage, Geoffrey; Hansford, Jordan R; Khuong-Quang, Dong-Anh; Gottardo, Nicholas G; Hassall, Timothy; Han, Jung Woo; Yalon Oren, Michal; Chi, Susan N; Qiu, Jiaheng; Da Costa, Daniel; Govinda Raju, Sandya; Manley, Peter; Hargrave, Darren

High-throughput in vitro drug screening and in vivo studies identify fenretinide as a brain-penetrant DMG therapeutic

高通量体外药物筛选和体内研究表明,芬瑞替尼是一种可穿透血脑屏障的DMG治疗药物。

Upton, Dannielle H; Liu, Jie; George, Sandra M; Valvi, Santosh; Ung, Caitlin; Rayner, Benjamin S; Gopalakrishnan, Anjana; Pandher, Ruby; Khan, Aaminah; Venkat, Pooja; Mayoh, Chelsea; Holliday, Holly; Yeung, Nicole; Nguyen, Hieu; Franshaw, Laura; Ehteda, Anahid; Shen, Han; Farruggia, Giovanna; Orienti, Isabella; Reynolds, C Patrick; Tsoli, Maria; Ziegler, David S

Beyond base camp: PI3K/mTOR inhibition for the treatment of pediatric high-grade gliomas

超越大本营:PI3K/mTOR抑制剂治疗儿童高级别胶质瘤

Duchatel, Ryan J; Savary, Clara; Germon, Zacary P; Riley, Madisen; Ziegler, David S; Mueller, Sabine; Jackson, Evangeline R; Dun, Matthew D

Arginine depletion potentiates standard-of-care chemo-immunotherapy in preclinical models of high-risk neuroblastoma.

在高危神经母细胞瘤的临床前模型中,精氨酸耗竭可增强标准治疗化疗免疫疗法的疗效

Hanssen Kimberley M, Murray Jayne, Pandher Ruby, Alfred Stephanie, Gamble Laura D, Brand Jennifer, Mosmann Erin, Kusuma Frances K, Mak Crystal, Kearns Adam, Kamili Alvin, Atkinson Caroline, Minchaca Alexis Z, Bertoldo Jean, Ziegler David S, Mussai Francis, Cheng Paul N M, Norris Murray D, Fletcher Jamie I, Haber Michelle

Clinical Characteristics and Outcomes of Central Nervous System Tumors Harboring NTRK Gene Fusions

携带NTRK基因融合的中枢神经系统肿瘤的临床特征和预后

Lamoureux, Audrey-Anne; Fisher, Michael J; Lemelle, Lauriane; Pfaff, Elke; Amir-Yazdani, Pouneh; Kramm, Christof; De Wilde, Bram; Kazanowska, Bernarda; Hutter, Caroline; Pfister, Stefan M; Sturm, Dominik; Jones, David T W; Orbach, Daniel; Pierron, Gaëlle; Raskin, Scott; Drilon, Alexander; Diamond, Eli L; Harada, Guilherme; Zapotocky, Michal; Zamecnik, Josef; Krskova, Lenka; Ellezam, Benjamin; Weil, Alexander G; Venne, Dominic; Barritault, Marc; Leblond, Pierre; Coltin, Hallie; Hammad, Rawan; Tabori, Uri; Hawkins, Cynthia; Hansford, Jordan R; Meyran, Deborah; Erker, Craig; McFadden, Kathryn; Sato, Mariko; Gottardo, Nicholas G; Dholaria, Hetal; Nørøxe, Dorte Schou; Goto, Hiroaki; Ziegler, David S; Lin, Frank Y; Parsons, Donald Williams; Lindsay, Holly; Wong, Tai-Tong; Liu, Yen-Lin; Wu, Kuo-Sheng; Franson, Andrea T; Hwang, Eugene; Aguilar-Bonilla, Ana; Cheng, Sylvia; Cacciotti, Chantel; Massimino, Maura; Schiavello, Elisabetta; Wood, Paul; Hoffman, Lindsey M; Cappellano, Andréa; Lassaletta, Alvaro; Van Damme, An; Llort, Anna; Gerber, Nicolas U; Spalato Ceruso, Mariella; Bendel, Anne E; Skrypek, Maggie; Hamideh, Dima; Mushtaq, Naureen; Walter, Andrew; Jabado, Nada; Alsahlawi, Aysha; Farmer, Jean-Pierre; Coleman, Christina; Mueller, Sabine; Mazewski, Claire; Aguilera, Dolly; Robison, Nathan J; O'Halloran, Katrina; Abbou, Samuel; Berlanga, Pablo; Geoerger, Birgit; Øra, Ingrid; Moertel, Christopher L; Razis, Evangelia D; Vernadou, Anastasia; Ducray, François; Bronnimann, Charlotte; Seizeur, Romuald; Clarke, Matthew; Resnick, Adam C; Alves, Mélanie; Jones, Chris; Doz, François; Laetsch, Theodore W; Perreault, Sébastien