In utero delivery of targeted ionizable lipid nanoparticles facilitates in vivo gene editing of hematopoietic stem cells.
子宫内递送靶向可电离脂质纳米颗粒有助于造血干细胞的体内基因编辑
期刊:Proceedings of the National Academy of Sciences of the United States of America
影响因子:9.1
doi:10.1073/pnas.2400783121
Palanki Rohan, Riley John S, Bose Sourav K, Luks Valerie, Dave Apeksha, Kus Nicole, White Brandon M, Ricciardi Adele S, Swingle Kelsey L, Xue Lulu, Sung Derek, Thatte Ajay S, Safford Hannah C, Chaluvadi Venkata S, Carpenter Marco, Han Emily L, Maganti Rohin, Hamilton Alex G, Mrksich Kaitlin, Billingsley Margaret B, Zoltick Philip W, Alameh Mohamad-Gabriel, Weissman Drew, Mitchell Michael J, Peranteau William H