CRISPR-Cas9 Engineered Extracellular Vesicles for the Treatment of Dominant Progressive Hearing Loss
CRISPR-Cas9 设计的细胞外囊泡可用于治疗显性进行性听力损失
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doi:10.1101/2023.09.14.557853
Xiaoshu Pan, Peixin Huang, Samantha S Ali, Bryan Renslo, Tarun E Hutchinson, Nina Erwin, Zachary Greenberg, Zuo Ding, Yanjun Li, Athanasia Warnecke, Natalia E Fernandez, Hinrich Staecker, Mei He