日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Multi-targeting zinc finger nuclease vector unsilences paternal UBE3A in a mouse model of Angelman syndrome

多靶点锌指核酸酶载体在安格曼综合征小鼠模型中解除父系UBE3A基因的沉默

Bazick, Hannah O; James, Lucas M; Taylor-Blake, Bonnie; Wolter, Justin M; Zylka, Mark J

Crossing the finish line towards a disease-modifying treatment for Angelman syndrome

距离研发出安格曼综合征的疾病改善疗法又近了一步

Judson, Matthew C; de Almeida, Luis Pereira; Burdine, Rebecca D; Chamberlain, Stormy J; Deverman, Benjamin E; Distel, Ben; Ehlers, Michael D; Jalazo, Elizabeth; Kushner, Steven A; Nespeca, Mark; Sanders, Stephan J; Scheffner, Martin; Yi, Jason J; Zylka, Mark J; Elgersma, Ype; Philpot, Benjamin D

CellPheno: A High-throughput Computational Platform for Quantifying Cellular Resolution Whole Brain Microscopy Images

CellPheno:用于量化细胞分辨率全脑显微图像的高通量计算平台

Wei, Ziquan; Curtin, Ian; Kyere, Felix A; Borland, David; Yi, Hong; Kim, Minjeong; Dere, Mustafa; McCormick, Carolyn M; Krupa, Oleh; Shih, Yen-Yu Ian; Zylka, Mark J; Stein, Jason L; Wu, Guorong

Chd8 haploinsufficiency leads to molecular layer heterotopias and age-dependent cortical expansion

Chd8单倍体不足会导致分子层异位和年龄依赖性皮质扩张。

Kyere, Felix A; Curtin, Ian; Wei, Ziquan; Yin, Maya Yilan; Xing, Lei; Wen, Tao; Vlasova, Roza M; Li, Kejia; Matoba, Nana; McCormick, Carolyn M; Farah, Tala; Krupa, Oleh; Glass, Madison R; Taylor-Blake, Bonnie; McCoy, Eric S; Wang, Tzu-Wen Winnie; He, Qiuhong; Dere, Mustafa; D'Arcy, Brooke R; Davis, Liam T; Dayananda, Veda; Escobar-Tomlienovich, Carla; Eswar, Karthik; Moghul, Maryam; Yeturi, Meghana; Huang, Karen; Baldonado, Micah; Kaikini, Mihir; Silver, Debra L; Borland, David; Yi, Hong; Ariel, Pablo; Shih, Yen-Yu Ian; Zylka, Mark J; Wu, Guorong; Stein, Jason L

The environmental neuroactive chemicals list of prioritized substances for human biomonitoring and neurotoxicity testing: A database and high-throughput toxicokinetics approach

用于人体生物监测和神经毒性测试的环境神经活性化学物质优先清单:数据库和高通量毒代动力学方法

Rager, Julia E; Koval, Lauren E; Hickman, Elise; Ring, Caroline; Teitelbaum, Taylor; Cohen, Todd; Fragola, Giulia; Zylka, Mark J; Engel, Lawrence S; Lu, Kun; Engel, Stephanie M

Evaluating the efficacy of neurokinin-1 (substance P) receptor antagonist CP-99994 on facial grimacing and allodynia in mice postsurgery: a comparative study with known analgesics

评估神经激肽-1(P物质)受体拮抗剂CP-99994对小鼠术后面部扭曲和痛觉过敏的疗效:与已知镇痛药的比较研究

McCoy, Eric S; Ryan, Dan F; Park, Sang Kyoon; Zylka, Mark J

AAV-dCas9 vector unsilences paternal Ube3a in neurons by impeding Ube3a-ATS transcription.

AAV-dCas9 载体通过抑制 Ube3a-ATS 转录来解除神经元中父系 Ube3a 的沉默

Wolter Justin M, James Lucas M, Boeshore Samantha L, Mao Hanqian, McCoy Eric S, Ryan Daniel F, Fragola Giulia, Taylor-Blake Bonnie, Stein Jason L, Zylka Mark J

A luminescence-based biosensor to measure endogenous UBE3A activity.

一种基于发光的生物传感器,用于测量内源性 UBE3A 活性。

Xing Lei, Lamberti Sophia U, Nourie Hannah C, Rust Trinity E, Hu Wenxin, Zylka Mark J

Compact Calm1 promoter enables AAV mediated neuron-targeted expression in human iPSC-derived brain organoids

紧凑型 Calm1 启动子可实现 AAV 介导的人类 iPSC 衍生脑类器官中神经元靶向表达

Klockner, Ina; Yeturi, Meghana; Rust, Trinity E; Stein, Jason L; Zylka, Mark J

Enhanced facial grimacing when laparotomy involves cutaneous and visceral tissue injury

剖腹手术涉及皮肤和内脏组织损伤时,面部表情会更加痛苦。

Shao, Minghao; McCoy, Eric S; Zylka, Mark J