Real-world data of Brazilian adults with X-linked hypophosphatemia (XLH) treated with burosumab and comparison with other worldwide cohorts
巴西接受布罗索单抗治疗的 X 连锁低磷血症 (XLH) 成年患者的真实世界数据,并与世界其他地区的队列进行比较
期刊:Molecular Genetics & Genomic Medicine
影响因子:1.6
doi:10.1002/mgg3.2387
Vaisbich, Maria Helena; de Cillo, Antônio César Paulillo; Silva, Bárbara Campolina C; DÁlva, Catarina Brasil; de Carvalho, Érico Higino; de Almeida, Juliana M C M; Marques, Larissa L M; Ribeiro, Marcia; da Silva, Mauro Borghi M; de Medeiros, Paula Frassinetti V; Mendes, Pedro Henrique