6-year treatment follow-up with an extended-release alkaline formulation (Sibnayal(®)) in primary distal renal tubular acidosis
使用缓释碱性制剂(Sibnayal®)治疗原发性远端肾小管酸中毒的6年随访研究
期刊:Orphanet Journal of Rare Diseases
影响因子:3.5
doi:10.1186/s13023-025-03953-4
Bertholet-Thomas, Aurélia; De Mul, Aurélie; Bernardor, Julie; Roussey-Kesler, Gwenaëlle; Podracka, Ludmila; Novo, Robert; Nobili, François; Knebelmann, Bertrand; Harambat, Jérôme; Golubovic, Emilija; Boyer, Olivia; Di Maio, Massimo; Cailliez, Mathilde; Baudouin, Véronique; Chidler, Laure; Leblanc, Véronique; Bacchetta, Justine