Triplet-repeat oligonucleotide-mediated reversal of RNA toxicity in myotonic dystrophy
三核苷酸重复寡核苷酸介导的逆转强直性肌营养不良症中的RNA毒性
期刊:Proceedings of the National Academy of Sciences of the United States of America
影响因子:9.1
doi:10.1073/pnas.0905780106
Mulders, Susan A M; van den Broek, Walther J A A; Wheeler, Thurman M; Croes, Huib J E; van Kuik-Romeijn, Petra; de Kimpe, Sjef J; Furling, Denis; Platenburg, Gerard J; Gourdon, Geneviève; Thornton, Charles A; Wieringa, Bé; Wansink, Derick G