日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Etranacogene dezaparvovec in people with hemophilia B with preexisting adeno-associated virus 5 neutralizing antibodies: 4-year subgroup results from the HOPE-B trial

在伴有预先存在的腺相关病毒5型中和抗体的B型血友病患者中应用依曲那康基因(Etranacogene dezaparvovec):HOPE-B试验的4年亚组结果

Klamroth, Robert; Monahan, Paul E; Van der Valk, Paul; Quon, Doris; Kazmi, Rashid Saeed; Coppens, Michiel; O'Connell, Niamh; Pipe, Steven W; von Drygalski, Annette; Afzal, Saira; Gabriel, Richard; Youssar, Loubna; Gill, Sean; Jansen, Nathalie; Wang, Fei; Le Quellec, Sandra; Hermans, Cedric

Health care resources and costs associated with delivering gene therapy for hemophilia in clinical practice

在临床实践中,为血友病患者提供基因治疗所涉及的医疗资源和成本

Prameyllawati, Diaz M; Mussert, Caroline M A; Oude Voshaar, Martijn A H; Lingsma, Hester F; Cnossen, Marjon H; Coppens, Michiel; Meijer, Karina; van der Valk, Paul R; Leebeek, Frank W G; Ten Ham, Renske M T

Predictors of Acute Exacerbations in COPD: A Systematic Review

慢性阻塞性肺疾病急性加重预测因素:系统评价

Chamaon, Dumiana; Lenferink, Anke; Bucsán, Charlotte; Van Dijk, Sanne H B; Van Beurden, Wendy J C; van der Valk, Paul D L P M; van der Palen, Job; Brusse-Keizer, Marjolein G J

Natural history of preexisting AAV5 antibodies in adults with hemophilia B during the lead-in of the etranacogene dezaparvovec phase 3 study

在etranacogene dezaparvovec 3期研究导入期,B型血友病成人患者体内已存在的AAV5抗体的自然史

Klamroth, Robert; Recht, Michael; Key, Nigel S; Miesbach, Wolfgang; Pipe, Steven W; Kaczmarek, Radoslaw; Drelich, Douglass; Salazar, Blanca; Le Quellec, Sandra; Monahan, Paul E; Galante, Nicholas; van der Valk, Paul; Tarrant, Jacqueline

Correlation of gene expression with magnetic resonance imaging features of retinoblastoma: a multi-center radiogenomics validation study

视网膜母细胞瘤基因表达与磁共振成像特征的相关性:一项多中心放射基因组学验证研究

Jansen, Robin W; Roohollahi, Khashayar; Uner, Ogul E; de Jong, Yvonne; de Bloeme, Christiaan M; Göricke, Sophia; Sirin, Selma; Maeder, Philippe; Galluzzi, Paolo; Brisse, Hervé J; Cardoen, Liesbeth; Castelijns, Jonas A; van der Valk, Paul; Moll, Annette C; Grossniklaus, Hans; Hubbard, G Baker; de Jong, Marcus C; Dorsman, Josephine; de Graaf, Pim

Does adherence to exacerbation action plans matter? Insights from two COPD self-management studies

遵守急性加重应对计划是否重要?来自两项慢性阻塞性肺病自我管理研究的启示

Schrijver, Jade; Effing, Tanja; van Helden, Joanke; van der Palen, Job; van der Valk, Paul; Brusse-Keizer, Marjolein; Lenferink, Anke

Exploring Patterns of COPD Exacerbations and Comorbid Flare-Ups

探索慢性阻塞性肺疾病急性加重和合并症发作的模式

van Dijk, Sanne H B; Brusse-Keizer, Marjolein G J; Effing, Tanja; van der Valk, Paul D L P M; Ploumen, Eline H; van der Palen, Job; Doggen, Carine J M; Lenferink, Anke

Liver-related complications before and after successful treatment of chronic hepatitis C virus infection in people with inherited bleeding disorders

遗传性出血性疾病患者成功治疗慢性丙型肝炎病毒感染前后肝脏相关并发症

Isfordink, Cas J; van Erpecum, Karel J; Fischer, Kathelijn; van der Valk, Paul R; van Vulpen, Lize F D; Schutgens, Roger E G; Arends, Joop E; Mauser-Bunschoten, Evelien P

Self-management interventions for people with chronic obstructive pulmonary disease

慢性阻塞性肺病患者的自我管理干预措施

Schrijver, Jade; Lenferink, Anke; Brusse-Keizer, Marjolein; Zwerink, Marlies; van der Valk, Paul Dlpm; van der Palen, Job; Effing, Tanja W

Reduced cardiovascular morbidity in patients with hemophilia: results of a 5-year multinational prospective study

降低血友病患者心血管疾病发病率:一项为期5年的多国前瞻性研究结果

Van Der Valk, Paul; Makris, Michael; Fischer, Kathelijn; Tait, Robert C; Chowdary, Pratima; Collins, Peter W; Meijer, Karina; van Vulpen, Lize F D; Mauser-Bunschoten, Eveline; Schutgens, Roger E G