日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

BCMA-directed mRNA CAR T cell therapy for myasthenia gravis: a randomized, double-blind, placebo-controlled phase 2b trial

BCMA靶向mRNA CAR T细胞疗法治疗重症肌无力:一项随机、双盲、安慰剂对照的2b期试验

Vu, Tuan; Durmus, Hacer; Rivner, Michael; Shroff, Sheetal; Ragole, Thomas; Myers, Bennett; Pasnoor, Mamatha; Small, George; Karam, Chafic; Vullaganti, Mithila; Peltier, Amanda; Sahagian, Gregory; Feinberg, Marc H; Slanksy, Adam; Barnett-Tapia, Carolina; Siddiqi, Zaeem; Gwathmey, Kelly; Badruddoja, Michael A; Kamboh, Hafsa; Ruggerie, Rachel N; Fedak, Renee R; Stewart, C Andrew; Kurtoglu, Metin; Kalayoglu, Murat; Singer, Michael; Jewell, Christopher M; Miljkovic, Milos D; Dimachkie, Mazen; Mozaffar, Tahseen; Howard, James F Jr

BCMA-directed mRNA CAR-T cell therapy for myasthenia gravis: exploratory biomarker analysis of a placebo-controlled phase 2b trial.

BCMA 靶向 mRNA CAR-T 细胞疗法治疗重症肌无力:安慰剂对照 2b 期试验的探索性生物标志物分析。

Fedak Renee R, Ruggerie Rachel N, Shan Yufei, Curvino Elizabeth J, de Sousa Juliana F, Daniel Shaji, Ngo-Casi Minhtran, Kamboh Hafsa, Vu Tuan, Durmuş Hacer, Mozaffar Tahseen, Howard James F Jr, English Emily P, Benson Albina, Duvernay Matthew T, Singer Michael S, Kalayoglu Murat V, Brunn Carsten, Bodansky Aaron, Anderson Mark S, DeRisi Joseph L, Garcia Samantha T, Yu David J L, Zorn Kelsey C, Kurtoglu Metin, Miljković Miloš D, Stewart C Andrew, Jewell Christopher M

Efficacy and Safety of Vemircopan in Generalized Myasthenia Gravis: A Randomized Clinical Trial

维米尔可泮治疗全身型重症肌无力的疗效和安全性:一项随机临床试验

Saccà, Francesco; Gialdini, Gino; Howard, James F Jr; Vu, Tuan H; Meisel, Andreas; Peric, Stojan; Lünemann, Jan D; Sgarzi, Manlio; Shaibani, Aziz; Bril, Vera; Yeh, Jiann-Horng; Reyes-Garrido, Virginia; Liao, Serena; Metais, Camille; van der Valk, Ralf J P

Elucidating genetic backgrounds of myasthenia gravis in Japanese by genome-wide association studies and multi-omics analyses of thymoma

通过全基因组关联研究和胸腺瘤多组学分析阐明日本重症肌无力的遗传背景

Ueda, Hiroyuki; Kubota, Tomoya; Goto, Risa; Suzuki, Akari; Ojima, Takafumi; Ogawa, Kotaro; Sonehara, Kyuto; Namba, Shinichi; Naito, Tatsuhiko; Wang, Qingbo; Konno, Shingo; Samukawa, Makoto; Kawaguchi, Naoki; Kimura, Takashi; Sugimoto, Takamichi; Murai, Hiroyuki; Yamawaki, Takemori; Kaida, Kenichi; Tokuyasu, Daiki; Yasuda, Manato; Akamine, Hiroyuki; Onishi, Yosuke; Ogawa, Yosuke; Shirai, Yuya; Edahiro, Ryuya; Yamamoto, Kenichi; Nagata, Hideki; Ose, Naoko; Takayama, Jun; Suzuki, Ken; Higashiue, Shinichi; Kobayashi, Shuzo; Yamaguchi, Hiroki; Okazaki, Yasushi; Matsumoto, Naoyuki; Motomura, Kenta; Koga, Hidenobu; Matsuda, Koichi; Tamiya, Gen; Yamamoto, Masayuki; Yamauchi, Toshimasa; Kadowaki, Takashi; Yamamoto, Kazuhiko; Ohno, Akiko; Okuno, Tatsusada; Morii, Eiichi; Mochizuki, Hideki; Nagane, Yuriko; Minami, Naoya; Uzawa, Akiyuki; Masuda, Masayuki; Suzuki, Shigeaki; Shimomura, Iichiro; Shintani, Yasushi; Utsugisawa, Kimiaki; Takahashi, Masanori P; Okada, Yukinori

BCMA/CD19 CAR T cell therapy for refractory myasthenia gravis: Proteomic signatures and single-cell transcriptomics of disease flares

BCMA/CD19 CAR T 细胞疗法治疗难治性重症肌无力:疾病发作的蛋白质组学特征和单细胞转录组学

Huang, Xiaoyu; Zhang, Zhouao; Liu, Dan; Luo, Tiancheng; An, Xueting; Yang, Mingjin; Li, Shengli; Wang, Gang; Li, Huizhong; Cao, Jiang; Sun, Zengtian; Du, Xue; Wang, Zhouyi; Guo, Xinyan; Ma, Tianyu; Peng, Deyou; Qi, Guoyan; Zong, Shenghua; Ding, Yanting; Cui, Guiyun; Shi, Ming; Zheng, Junnian; Zhang, Yong

Multi-omics profiling reveals intrathymic triggers and novel biomarkers in thymoma-associated myasthenia gravis

多组学分析揭示胸腺瘤相关重症肌无力的胸腺内触发因素和新型生物标志物

Ao, Yongqiang; Gao, Jian; Ying, Zhen; Wang, Shuai; Han, Zheng; Xia, Mingyu; Wen, Jiazhe; Zhu, Junkan; Wang, Caiying; Fu, Minjie; Jiang, Jiahao; Wang, Haikun; Dong, Jihong; Fan, Hong; Ding, Jianyong

Economic Evaluation of Thymectomy for the Treatment of Nonthymomatous Myasthenia Gravis

胸腺切除术治疗非胸腺瘤型重症肌无力的经济评价

Lord, Joseph; Walton, Matthew; Murphy, Peter; Shepherd, Lucy; Wolfe, Gil I; Sussman, Jon; Cutter, Gary; Kaminski, Henry; Aban, Inmaculada; Hamedani, Ali G; Hodgson, Robert

Efficacy and safety of immunosuppressants and immunomodulators in juvenile myasthenia gravis: a systematic review and meta-analysis

免疫抑制剂和免疫调节剂治疗幼年型重症肌无力的疗效和安全性:系统评价和荟萃分析

Zhong, Xiaoling; Xie, Yu; Li, YanMei; Yang, Hua; Luo, Rong

Targeting pathogenic Th17.1 cells via JAK-STAT3 pathway: A novel approach with tofacitinib for refractory myasthenia gravis

通过JAK-STAT3通路靶向致病性Th17.1细胞:托法替尼治疗难治性重症肌无力的新方法

Zhao, Rui; Yan, Chong; Zhong, Huahua; Huan, Xiao; Jin, Lei; He, Dingxian; Xi, Jianying; Li, Yarong; Xiao, Baoguo; Luo, Feifei; Zhao, Chongbo; Song, Jie; Luo, Sushan

Novel therapies for myasthenia gravis: Translational research from animal models to clinical application

重症肌无力的新疗法:从动物模型到临床应用的转化研究

Sorrenti, Benedetta; Laurini, Christian; Bosco, Luca; Strano, Camilla Mirella Maria; Ratti, Adele; Falzone, Yuri Matteo; Previtali, Stefano Carlo