DNA-PKcs inhibitor AZD7648 reveals sgRNA cross-contaminants and enhanced sensitivity of genome engineering off-target activity in HSPCs
DNA-PKcs抑制剂AZD7648揭示了sgRNA交叉污染,并增强了造血干细胞中基因组工程脱靶活性的敏感性
期刊:Nucleic Acids Research
影响因子:13.1
doi:10.1093/nar/gkag318
White, Nathan; Hu, Yi-Ting; Chalk, John Alexander; Kurgan, Gavin; Naseem, Asma; Schmaljohn, Ellen; Sturgeon, Morgan; Cavazza, Alessia; Thrasher, Adrian James; Turchiano, Giandomenico