日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Development of a DUX4-targeting antibody oligonucleotide conjugate as a therapy for FSHD

开发靶向DUX4的抗体寡核苷酸偶联物作为FSHD的治疗方法

Malecova, Barbora; Sala, David; Melikian, Garineh M; Johns, Rachel; Erdogan, Gulin; Hartmann, Marc; Jordan, Maryam; Arias, Joel Danny; Bhattacharya, Arvind; Meng, Qingying; Dansereau, Oliver; Beppler, Samuel W; Doppalapudi, Venkata R; Huang, Hanhua; Flanagan, William Michael; Levin, Arthur A

DUX4-induced HSATII RNA accumulation drives protein aggregation, impacting RNA processing pathways.

DUX4 诱导的 HSATII RNA 积累驱动蛋白质聚集,影响 RNA 加工途径。

Arends Tessa, Bennett Sean R, Tapscott Stephen J

DUX4 reduction and muscle function improvement by subcutaneous delivery of gapmer antisense oligonucleotides

皮下注射 gapmer 反义寡核苷酸可降低 DUX4 水平并改善肌肉功能

Zhang, Aiping; Lim, Kenji Rowel Q; Chen, Ze; Yokota, Toshifumi; Chen, Yi-Wen

Superficially located CIC::DUX4-rearranged sarcomas in children: insights from a long-term survival case series

儿童浅表性CIC::DUX4重排肉瘤:来自长期生存病例系列的启示

Del Vecchio, Gina; Alaggio, Rita; Stracuzzi, Alessandra; Gaggero, Gabriele; Giovannoni, Isabella; Barresi, Sabina; Rossi, Sabrina; Arienzo, Francesca; Milano, Giuseppe Maria; Russo, Ida; Di Prete, Monia; Cota, Carlo; Cesen, Maja; Davis, Jessica L; Orbach, Daniel; Arciuolo, Damiano

[Clinical characteristics of DUX4-IGH fusion B-cell acute lymphoblastic leukemia in children]

[儿童DUX4-IGH融合基因B细胞急性淋巴细胞白血病的临床特征]

Luo, Yu-Xuan; Jiang, Hua; Wang, Jia-Yi; Hao, Wen-Ge; Zhang, Wei-Na

Identification of compounds that repress DUX4 expression in facioscapulohumeral muscular dystrophy

鉴定抑制面肩肱型肌营养不良症中DUX4表达的化合物

Chang, Ning; Moore, Hannah P; Himeda, Charis L; O'Brien, Terrence E; Thomas, William; Roshanravan, Baback; Jones, Takako I; Jones, Peter L

Modeling CIC::DUX4 sarcoma reveals oncogene-mediated MHCI-dependent immune evasion.

CIC::DUX4 肉瘤模型揭示了癌基因介导的 MHCI 依赖性免疫逃逸。

Vachanaram Ajay Ram, Wei Erdong, Mitanoska Ana, Bassett William, Kyba Michael, Bosnakovski Darko

Small round cell sarcoma tumoroid biobank reveals CIC::DUX4 sarcoma vulnerability to MCL-1 inhibition

小圆细胞肉瘤类肿瘤生物样本库揭示了CIC::DUX4肉瘤对MCL-1抑制剂的敏感性

Femke C A S Ringnalda ,Gijs J F van Son ,Laurens H G Verweij ,Seok-Young Kim ,Vicky Amo-Addae ,Uta E Flucke ,Laura S Hiemcke-Jiwa ,Karin P S Langenberg ,Jos A M Bramer ,Lotte Heimans ,Michiel A J van de Sande ,Winan J van Houdt ,Max M van Noesel ,Hinri H D Kerstens ,Marcel Santoso ,Georg Seifert ,Olivier Delattre ,Katia Scotlandi ,Birgit Geoerger ,Johannes H M Merks ,Jan J Molenaar ,Ruben van Boxtel ,Marc van de Wetering ,Karin Sanders # ,Hans Clevers #

DUX4-rearranged B-ALL: deciphering a biological and clinical conundrum

DUX4重排的B-ALL:破解生物学和临床难题

Bakewell, Jack; Moorman, Anthony V; Ryan, Sarra L

Erratum for the Research Article "DUX4-r exerts a neomorphic activity that depends on GTF2I in acute lymphoblastic leukemia" by D. Campolungo et al

D. Campolungo 等人的研究论文“DUX4-r 在急性淋巴细胞白血病中发挥依赖于 GTF2I 的新功能”的勘误