Severe Toxicity in Nonhuman Primates and Piglets Following High-Dose Intravenous Administration of an Adeno-Associated Virus Vector Expressing Human SMN
大剂量静脉注射表达人类 SMN 的腺相关病毒载体后，非人类灵长类动物和猪仔产生严重毒性
期刊:Human Gene Therapy
影响因子:3.9
doi:10.1089/hum.2018.015
Christian Hinderer, Nathan Katz, Elizabeth L Buza, Cecilia Dyer, Tamara Goode, Peter Bell, Laura K Richman, James M Wilson
