日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Sustained Benefit of Blinatumomab in Infants With KMT2A-Rearranged ALL: Long-Term Outcomes, Toxicity, and Pharmacokinetics

Blinatumomab 对 KMT2A 重排 ALL 患儿的持续疗效:长期结果、毒性和药代动力学

Vieira Martins, Miguel; de Lorenzo, Paola; Kotecha, Rishi S; Attarbaschi, Andishe; Escherich, Gabriele; Nysom, Karsten; Stary, Jan; Ferster, Alina; Brethon, Benoit; Locatelli, Franco; Schrappe, Martin; Scholte-van Houtem, Peggy E; Valsecchi, Maria G; Huitema, Alwin D R; Pieters, Rob; van der Sluis, Inge M

Off-the-shelf dual CAR-iNKT cell immunotherapy eradicates medullary and leptomeningeal high-risk KMT2A-rearranged leukemia

现成的双重CAR-iNKT细胞免疫疗法可根除髓质和软脑膜高危KMT2A重排白血病

Ren, Hongwei; Elliott, Natalina; Lye, Bryan; Sharif Shohan, Mohammad Umer; Cross, Joe W; Field, Lucy; Ponnusamy, Kanagaraju; Rice, Siobhan; Jackson, Thomas; Leontari, Ilia; El Ouazzani, Nouhad; Thomas, Rebecca; Inglott, Sarah; Bartram, Jack; Smith, Owen; Bond, Jonathan; Roberts, Irene A G; Halsey, Christina; Bashford-Rogers, Rachael; Milne, Thomas A; Roy, Anindita; Karadimitris, Anastasios

A microRNA expression signature in infant t(4;11) KMT2A::AFF1+ BCP-ALL uncovers novel therapeutic targets

婴儿t(4;11) KMT2A::AFF1+ BCP-ALL中的microRNA表达特征揭示了新的治疗靶点

Malouf, Camille; Duguid, Alasdair; Vrenken, Kirsten S; Leah, Tom; Medhi, Ragini; Camiolo, Giuseppina; Nitsche, Leslie; Jakobczyk, Hélène; Kotecha, Rishi S; Anderson, Richard A; Barrett, Neil A; Smith, Owen P; Stam, Ronald W; Ottersbach, Katrin

A microRNA expression signature in infant t(4;11) KMT2A::AFF1+ BCP‐ALL uncovers novel therapeutic targets

婴儿 t(4;11) KMT2A::AFF1+ BCP-ALL 中的 microRNA 表达特征揭示了新的治疗靶点

Papadopoulou, Anastasia; Alvanou, Maria; Karavalakis, George; Tzannou, Ifigeneia; Yannaki, Evangelia; Malouf, Camille; Duguid, Alasdair; Vrenken, Kirsten S; Leah, Tom; Medhi, Ragini; Camiolo, Giuseppina; Nitsche, Leslie; Jakobczyk, Hélène; Kotecha, Rishi S; Anderson, Richard A; Barrett, Neil A; Smith, Owen P; Stam, Ronald W; Ottersbach, Katrin

Intra-subtype heterogeneity shapes treatment response in KMT2A-rearranged ALL across all age groups

亚型内异质性影响所有年龄组中KMT2A重排ALL的治疗反应

Hartmann, Alina M; Bastian, Lorenz; Barz, Malwine J; Haas, Johannes; Amelunxen, Eric; Ehm, Patrick; Lenk, Lennart; Kotrova, Michaela; Beder, Thomas; Steffen, Fabio D; Rauwolf, Kerstin; Wolgast, Nadine; Bendig, Sonja; Bozzetti, Cecilia; Alten, Julia; Mondal, Mayukh; Rademacher, Annika; Heymann, Julia; Walter, Wencke; Haferlach, Claudia; Ströh, Aeint-Steffen; Bergmann, Anke K; Burmeister, Thomas; Gökbuget, Nicola; Bornhauser, Beat; Bourquin, Jean-Pierre; Brüggemann, Monika; Schrappe, Martin; Cario, Gunnar; Baldus, Claudia D

Age-specific mutation profiles and their prognostic implications in pediatric KMT2A-rearranged acute myeloid leukemia

儿童KMT2A重排急性髓系白血病中年龄特异性突变谱及其预后意义

Shoji, Kota; Yoshida, Kenichi; Iyoda, Shinju; Ishikawa, Moe; Tanaka, Miu; Nobe, Michidai; Saito, Nijika; Shino, Yuto; Nannya, Yasuhito; Yamato, Genki; Tsujimoto, Shinichi; Shiba, Norio; Hayashi, Yasuhide; Shiozawa, Yusuke; Shiraishi, Yuichi; Chiba, Kenichi; Okada, Ai; Tanaka, Hiroko; Miyano, Satoru; Koga, Yuhki; Goto, Hiroaki; Terui, Kiminori; Ito, Etsuro; Kiyokawa, Nobutaka; Tomizawa, Daisuke; Taga, Takashi; Moritake, Hiroshi; Tawa, Akio; Takita, Junko; Nishikori, Momoko; Adachi, Souichi; Ogawa, Seishi; Matsuo, Hidemasa

Clinical outcomes of older patients with NPM1-mutated or KMT2A-rearranged AML before menin inhibitors: a Beat AML report

在接受menin抑制剂治疗前,NPM1突变或KMT2A重排的AML老年患者的临床结局:Beat AML报告

Zeidner, Joshua F; Jain, Jayanshu; Welkie, Rina Li; Huang, Ying; Swords, Ronan T; Traer, Elie; Stein, Eytan M; Lin, Tara L; Madanat, Yazan F; Collins, Robert H; Baer, Maria R; Duong, Vu H; Blum, William G; Arellano, Martha L; Stock, Wendy; Odenike, Olatoyosi; Olin, Rebecca L; Smith, Catherine C; Foran, James M; Schiller, Gary J; Curran, Emily K; Handa, Shivani; Heerema, Nyla A; Chen, Timothy; Martycz, Molly; Stefanos, Mona; Marcus, Sonja G; Rosenberg, Leonard; Druker, Brian J; Levine, Ross L; Burd, Amy; Yocum, Ashley O; Mims, Alice S; Byrd, John C; Borate, Uma

Absence of Ledgf in mouse brain affects the Kmt2a/b and polycomb balance, synaptic transmission and motor function.

小鼠脑中 Ledgf 的缺失会影响 Kmt2a/b 和多梳蛋白的平衡、突触传递和运动功能。

Debusschere Laura, Bentea Eduard, Iglesias-Herrero Cecilia, Peredo Nicolas, Van Belle Siska, Van der Veken Nam Joo, Barber-Janer Anna, Plessers Dieter, Peelaerts Wouter, Hannes Wout, Michiels Martine, Van den Haute Chris, Baekelandt Veerle, Debyser Zeger

Targeting the Menin-KMT2A interaction in leukemia: Lessons learned and future directions

靶向治疗白血病中的 Menin-KMT2A 相互作用:经验教训与未来方向

Perner, Florian; Gadrey, Jayant Y; Armstrong, Scott A; Kühn, Michael W M

The hidden regulators: Non-coding RNAs in KMT2A-rearranged acute lymphoblastic leukemia

隐藏的调控因子:KMT2A重排急性淋巴细胞白血病中的非编码RNA

Poersch, Maria Augusta; Rodrigues, Ana Carolina; Stricker, Priscila Elias Ferreira; Azevedo, Alexandre Luiz Korte; Bruschi, Daniel Pacheco; de Oliveira, Jaqueline Carvalho