日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Long-Term Tofersen in SOD1 Amyotrophic Lateral Sclerosis

托弗森治疗SOD1肌萎缩侧索硬化症的长期疗效

Miller, Timothy M; Cudkowicz, Merit E; Shaw, Pamela J; Genge, Angela; Sobue, Gen; Bucelli, Robert C; Chiò, Adriano; Van Damme, Philip; Ludolph, Albert C; Glass, Jonathan D; Andrews, Jinsy A; Babu, Suma; Benatar, Michael; McDermott, Christopher J; Salachas, François; Bruneteau, Gaëlle; Al-Chalabi, Ammar; Amorin, Matthew; Nestorov, Ivan; Graham, Danielle; Lin, Luan; Sun, Peng; McNeill, Manjit; Malek, Sohail; Inra, Jennifer; Garafalo, Steve; Fradette, Stephanie

Impaired nucleocytoplasmic transport in SOD1-mediated ALS.

SOD1介导的ALS中核质转运受损。

Argueti-Ostrovsky Shirel, Lim Su Min, Arogundade Olubankole A, Diaz-Garcia Sandra, Yunisova Gulshan, Meng Alex, Hermann Anita, Ong Kailee, Eremenko Ekaterina, Bravo-Hernandez Mariana, Driscoll Shawn P, Lee Chao-Zong, Jiang Xin, Stavsky Alexandra, Barel Shir, Shani Tom, Kahn Joy, Pfaff Samuel L, Monsonego Alon, Marsala Martin, Ravits John, Lagier-Tourenne Clotilde, Israelson Adrian

SOD1 lactylation impair its enzymatic activity by conformational change to aggravate intervertebral disc degeneration.

SOD1 乳酸化通过构象变化损害其酶活性,从而加剧椎间盘退变。

Zhang Yuyao, Zhai Yu, Liu Chao, Chen Minghang, Zhang Yang, Bian Zhiqun, Chang Xian, Hu Zhilei, Li Jianmin, Zhang Chao, Ni Zhenhong, Xie Yangli, Chen Lin, Liu Minghan, Li Changqing

Microglial HVCN1 Deficiency Improves Movement and Survival of SOD1(G93A) ALS Mice by Enhancing Microglial Migration and Neuroprotection.

小胶质细胞 HVCN1 缺乏通过增强小胶质细胞迁移和神经保护作用改善 SOD1(G93A) ALS 小鼠的运动和存活率。

Wang Fan, Zhang Ke-Yu, Zhu Lang-Jian, Li Wei-Jue, Wu Yang, Gao Xiang, Ma Xiao-Ru, Yin Xiu-Hua, Wu Jian-Bin, Ye Xiao-Kang, Dong Zhao-Jun, Wang Di-Xian, Zhou Zhe, Wang Shao-Dong, Han Lei, Jiang Zhi-Nong, Zhao Jing-Wei

In vivo self-assembled SOD1-siRNAs mitigate muscle atrophy and denervation in amyotrophic lateral sclerosis

体内自组装SOD1-siRNA可减轻肌萎缩侧索硬化症中的肌肉萎缩和神经支配丧失

Guo, Jingwei; Zou, Qian; Xu, Jiawei; Lei, Jieqiong; Yin, Xin; Li, Botao; Fu, Jinyu; Mi, Junjie; Wang, Yanbo; Huang, Huan; Zhang, Chen-Yu; Chen, Xi

Neuropathological analysis of an ALS patient carrying a SOD1 missense variant and a C9orf72 repeat expansion

对一名携带 SOD1 错义变异和 C9orf72 重复扩增的 ALS 患者进行神经病理学分析

Miki, Tomoko; De Bertier, Sibylle; Amador, Maria-Del-Mar; Nicolas, Mélusine; Guissart, Claire; Deret, Marion; Teyssou, Elisa; Muratet, François; Bohl, Delphine; Lobsiger, Christian S; Boillée, Séverine; Esselin, Florence; Salachas, François; Millecamps, Stéphanie; Seilhean, Danielle

Reply to "Extending the Interpretation of Biomarker Dynamics in SOD1-ALS Proteomics"

回复“扩展SOD1-ALS蛋白质组学中生物标志物动态的解释”

Steffke, Christina; Brenner, David; Catanese, Alberto

Nose-to-brain delivery of a SOD1-stabilizing small molecule ameliorates pathology in an ALS mouse model

鼻脑递送SOD1稳定小分子可改善ALS小鼠模型的病理状况

Dhandapani, Ranjithkumar; Bakavayev, Shamchal; Armoza, Anna; Bersudsky, Marina; Shlifer, Arina; Yehezkel, Galit; Tsitrina, Alexandra; Barak, Zeev; Sintov, Amnon C; Engel, Stanislav

Validation in Drosophila of the in silico predicted clomipramine as repurposable for SOD1-ALS.

在果蝇中验证计算机预测的氯米帕明可用于治疗 SOD1-ALS。

Liguori Francesco, Amadio Susanna, Angioli Chiara, Ferriero Angelo, Passaro Iolanda, Alberti Francesca, Vernì Fiammetta, Volonté Cinzia

Reduced osteogenic factors and early osteoblast senescence in SOD1(G93A) ALS mouse model.

SOD1(G93A) ALS 小鼠模型中成骨因子减少和成骨细胞早期衰老。

Özkan Burak, Ramge Jan-Moritz, Wiesner Diana, Scekic-Zahirovic Jelena, Antonucci Stefano, Nungeß Sandra, Gebauer Dorothea, Ignatius Anita, Weishaupt Jochen H, Haffner-Luntzer Melanie, Roselli Francesco