日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Base editing HbS to HbG-Makassar improves hemoglobin function supporting its use in sickle cell disease

将HbS碱基编辑为HbG-Makassar可改善血红蛋白功能,支持其在镰状细胞病中的应用。

Zachary Kostamo # ,Manuel A Ortega # ,Chavonna Xu ,Patricia R Feliciano ,Elizabeth Budak ,Daisy Lam ,Valerie Winton ,Rebecca Jenkins ,Archita Venugopal ,Margaret Zhang ,John Jamieson ,Brent Coisman ,Kennedy Goldsborough ,Britney Hernandez ,Celeste K Kanne ,Erica N Evans ,Jordan Zgodny ,Yankai Zhang ,Jawa Darazim ,Ashwin Patel ,Michael A Pendergast ,John Manis ,Adam J Hartigan ,Giuseppe Ciaramella ,Seung-Joo Lee ,S Haihua Chu ,Vivien A Sheehan

Introducing a hemoglobin G-Makassar variant in HSCs by in vivo base editing treats sickle cell disease in mice

通过体内碱基编辑将血红蛋白G-Makassar变体引入造血干细胞可治疗小鼠镰状细胞病。

Chang Li ,Aphrodite Georgakopoulou ,Kiriaki Paschoudi ,Anna K Anderson ,Lishan Huang ,Sucheol Gil ,Maria Giannaki ,Efthymia Vlachaki ,Gregory A Newby ,David R Liu ,Evangelia Yannaki ,Hans-Peter Kiem ,André Lieber

Ccrk-Mak/Ick signaling is a ciliary transport regulator essential for retinal photoreceptor survival

Ccrk-Mak/Ick信号通路是纤毛运输调节因子,对视网膜感光细胞的存活至关重要。

Taro Chaya,Yamato Maeda,Ryotaro Tsutsumi,Makoto Ando,Yujie Ma,Naoko Kajimura,Teruyuki Tanaka,Takahisa Furukawa

PlasmidMaker is a versatile, automated, and high throughput end-to-end platform for plasmid construction

PlasmidMaker 是一个功能全面、自动化程度高、通量高的端到端质粒构建平台。

Behnam Enghiad # ,Pu Xue # ,Nilmani Singh ,Aashutosh Girish Boob ,Chengyou Shi ,Vassily Andrew Petrov ,Roy Liu ,Siddhartha Suryanarayana Peri ,Stephan Thomas Lane ,Emily Danielle Gaither ,Huimin Zhao

V. cholerae MakA is a cholesterol-binding pore-forming toxin that induces non-canonical autophagy

霍乱弧菌 MakA 是一种胆固醇结合成孔毒素,可诱导非经典自噬。

Xiaotong Jia ,Anastasia Knyazeva ,Yu Zhang ,Sergio Castro-Gonzalez ,Shuhei Nakamura ,Lars-Anders Carlson ,Tamotsu Yoshimori ,Dale P Corkery ,Yao-Wen Wu

Geniposide from Gardenia jasminoides var. radicans Makino Attenuates Myocardial Injury in Spontaneously Hypertensive Rats via Regulating Apoptotic and Energy Metabolism Signalling Pathway

栀子苷(Gerniposide from Gardenia jasminoides var. radicans Makino)通过调节细胞凋亡和能量代谢信号通路减轻自发性高血压大鼠的心肌损伤

Ying Hou # ,Peipei Yuan # ,Yang Fu ,Qi Zhang ,Liyuan Gao ,Yaxin Wei ,Xiaoke Zheng ,Weisheng Feng