A call for an integrated approach to improve efficiency, equity and sustainability in rare disease research in the United States

呼吁采取综合方法,提高美国罕见病研究的效率、公平性和可持续性

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Abstract

To build a more efficient, equitable, and sustainable approach to rare disease research in the United States, we must prioritize integrated research infrastructure and approaches that focus on understanding connections across rare diseases.

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