FITM2-Related Siddiqi Syndrome in Two Iranian Siblings

两名伊朗兄妹患有与FITM2相关的西迪基综合征

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Abstract

We report the first two Iranian siblings with Siddiqi syndrome, carrying a novel likely pathogenic FITM2 variant. Both presented with hallmark features, including early-onset sensorineural hearing loss, severe generalized dystonia, growth failure, and ichthyosis of the lower limbs, expanding the geographic and genetic spectrum of this rare disorder.

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