IgG-cleaving endopeptidase enables in vivo gene therapy in the presence of anti-AAV neutralizing antibodies
IgG 裂解内肽酶可在抗 AAV 中和抗体存在的情况下进行体内基因治疗
期刊:Nature Medicine
影响因子:58.7
doi:10.1038/s41591-020-0911-7
Christian Leborgne #, Elena Barbon #, Jeffrey M Alexander #, Hayley Hanby, Sandrine Delignat, Daniel M Cohen, Fanny Collaud, Saghana Muraleetharan, Dan Lupo, Joseph Silverberg, Karen Huang, Laetitia van Wittengerghe, Béatrice Marolleau, Adeline Miranda, Anna Fabiano, Victoria Daventure, Heena Beck,