日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

SCN10A-short gene therapy to restore conduction and protect against malignant cardiac arrhythmias

SCN10A短基因疗法可恢复传导功能并预防恶性心律失常

Wang, Jianan; Verkerk, Arie O; Wilders, Ronald; Zhang, Yingnan; Zhang, Kelly; Prakosa, Adityo; Rivaud, Mathilde R; Marsman, E Madelief J; Boender, Arie R; Klerk, Mischa; Fokkert, Lianne; de Jonge, Berend; Neef, Klaus; Kirzner, Osne F; Bezzina, Connie R; Remme, Carol Ann; Tan, Hanno L; Boukens, Bastiaan J; Devalla, Harsha D; Trayanova, Natalia A; Christoffels, Vincent M; Barnett, Phil; Boink, Gerard J J

PITX2 dosage-dependent changes in pacemaker cell state underlie sinus node dysfunction and atrial arrhythmias.

PITX2 剂量依赖性地改变起搏细胞状态是窦房结功能障碍和心房心律失常的根本原因。

van der Maarel Lieve E, Mungroo M Ridwane, Mulleners Otto J, Rivaud Mathilde R, Verkerk Arie O, van Duijvenboden Karel, Tiel Groenestege Freek H T, Steimle Jeffrey D, Fokkert Lianne, de Gier-de Vries Corrie, Klerk Mischa, Boender Arie R, Martin James F, Jensen Bjarke, Boink Gerard J J, Devalla Harsha D, Christoffels Vincent M

Living myocardial slices as a model for testing cardiac pro-reparative gene therapies.

以活体心肌切片为模型,测试心脏促修复基因疗法

Caliandro Rocco, Husetić Azra, Ligtermoet Merel L, Boender Arie R, Zentilin Lorena, Boink Gerard J J, Giacca Mauro, Gladka Monika M

Cross-species comparison reveals that Hmga1 reduces H3K27me3 levels to promote cardiomyocyte proliferation and cardiac regeneration

跨物种比较表明,Hmga1通过降低H3K27me3水平来促进心肌细胞增殖和心脏再生。

Mara Bouwman # ,Dennis E M de Bakker # ,Hessel Honkoop ,Alexandra E Giovou ,Danielle Versteeg ,Arie R Boender ,Phong D Nguyen ,Merel Slotboom ,Daniel Colquhoun ,Marta Vigil-Garcia ,Lieneke Kooijman ,Rob Janssen ,Ingeborg B Hooijkaas ,Marie Günthel ,Kimberly J Visser ,Mischa Klerk ,Lorena Zentilin ,Mauro Giacca ,Jan Kaslin ,Gerard J J Boink ,Eva van Rooij ,Vincent M Christoffels ,Jeroen Bakkers

AAV6 vectors provide superior gene transfer compared to AAV9 vectors following intramyocardial administration.

与 AAV9 载体相比,AAV6 载体在心肌内注射后可提供更优的基因转移效果

Wang Jianan, Jonker Timo, Cervera-Barea Aina, Dong Zhenyu, Visser Ruud N, Birza Evelien E, Boender Arie R, Klerk Mischa, Yang Yuting, Visser Joyce, Jansen Marlijn S, Grootswagers Tom C, Bart Cindy I, de Jager Saskia C A, Schrödel Silke, Thirion Christian, Kirzner Osne F, Tan Hanno L, de Vries Antoine A F, Sluijter Joost P G, Neef Klaus, de Groot Joris R, Christoffels Vincent M, Boink Gerard J J

New views on the complex interplay between degeneration and autoimmunity in multiple sclerosis

关于多发性硬化症中退行性变和自身免疫之间复杂相互作用的新观点

Stys, Peter K; Tsutsui, Shigeki; Gafson, Arie R; 't Hart, Bert A; Belachew, Shibeshih; Geurts, Jeroen J G

Burdens of infection control on healthcare workers: a scoping review

感染控制对医护人员的负担:一项范围界定综述

Ungar, R; Gur-Arie, R; Heriot, G S; Jamrozik, E

Genome-wide study of longitudinal brain imaging measures of multiple sclerosis progression across six clinical trials

一项涵盖六项临床试验的多发性硬化症进展纵向脑成像指标的全基因组研究

Loomis, Stephanie J; Sadhu, Nilanjana; Fisher, Elizabeth; Gafson, Arie R; Huang, Yunfeng; Yang, Chengran; Hughes, Emily E; Marshall, Eric; Herman, Ann; John, Sally; Runz, Heiko; Jia, Xiaoming; Bhangale, Tushar; Bronson, Paola G

Serum Neurofilament Light and Multiple Sclerosis Progression Independent of Acute Inflammation

血清神经丝轻链与多发性硬化症进展无关,与急性炎症无关

Gafson, Arie R; Jiang, Xiaotong; Shen, Changyu; Kapoor, Raj; Zetterberg, Henrik; Fox, Robert J; Belachew, Shibeshih

Safety, Patient-Reported Well-Being, and Physician-Reported Assessment of Walking Ability in Patients with Multiple Sclerosis for Prolonged-Release Fampridine Treatment in Routine Clinical Practice: Results of the LIBERATE Study

LIBERATE 研究结果:多发性硬化症患者在常规临床实践中使用缓释法莫吡啶治疗的安全性、患者自述健康状况和医生评估的步行能力

Castelnovo, Giovanni; Gerlach, Oliver; Freedman, Mark S; Bergmann, Arnfin; Sinay, Vladimiro; Castillo-Triviño, Tamara; Kong, George; Koster, Thijs; Williams, Heather; Gafson, Arie R; Killestein, Joep