日期 影响因子
日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:
–

Age-sensitive response of systemic AAV-mediated gene therapy in a newly characterized feline model of mucolipidosis II.

在新鉴定的猫粘脂病 II 型模型中，系统性 AAV 介导的基因治疗的年龄敏感性反应

期刊:Molecular Therapy
影响因子:12
doi:10.1016/j.ymthe.2025.04.030
Pyne Nettie K, Bagel Jessica, Shyng Charles, Odonnell Patricia, Miyadera Keiko, Srnak Jennifer, Swain Gary, Pesayco Jill P, Shelton G Diane, Assenmacher Charles-Antoine, Dickson Patricia, Stern Joshua A, Flanagan-Steet Heather, Gray Steven J, Bradbury Allison M
Feline
发表日期：2025
文献求助 收藏

Adeno-associated vector corneal gene therapy reverses corneal clouding in a feline model of mucopolysaccharidosis VI

腺相关载体角膜基因疗法逆转了猫粘多糖贮积症VI型模型中的角膜混浊

期刊:PLoS One
影响因子:2.6
doi:10.1371/journal.pone.0338370
Gilger, Brian C; Song, Liujiang; Hasegawa, Tomoko; Salmon, Jacklyn H; Bower, Jacquelyn J; Vridhachalam, Naveen; Collins, Elisabeth; Roberts, Darby; Bagel, Jessica; Molony, Caitlyn; Vite, Charles; Hirsch, Matthew L
发表日期：2025
文献求助 收藏

Cerebrospinal fluid and serum glycosphingolipid biomarkers in canine globoid cell leukodystrophy (Krabbe Disease)

犬球状细胞脑白质营养不良症（克拉伯病）脑脊液和血清糖鞘脂生物标志物

期刊:Molecular and Cellular Neuroscience
影响因子:
doi:10.1016/j.mcn.2019.103451
Corado, Carley R; Pinkstaff, Jason; Jiang, Xuntian; Galban, Evelyn M; Fisher, Samantha J; Scholler, Oriane; Russell, Chris; Bagel, Jessica H; ODonnell, Patricia A; Ory, Daniel S; Vite, Charles H; Bradbury, Allison M
细胞生物学
神经科学
发表日期：2020
文献求助 收藏

Evaluation of Intrathecal Routes of Administration for Adeno-Associated Viral Vectors in Large Animals

大型动物腺相关病毒载体鞘内给药途径的评价

期刊:Human Gene Therapy
影响因子:4
doi:10.1089/hum.2017.026
Hinderer, Christian; Bell, Peter; Katz, Nathan; Vite, Charles H; Louboutin, Jean-Pierre; Bote, Erin; Yu, Hongwei; Zhu, Yanqing; Casal, Margret L; Bagel, Jessica; O'Donnell, Patricia; Wang, Ping; Haskins, Mark E; Goode, Tamara; Wilson, James M
微生物学
发表日期：2018
文献求助 收藏

Clinical Improvement of Alpha-mannosidosis Cat Following a Single Cisterna Magna Infusion of AAV1

单次经枕大池输注AAV1后，α-甘露糖苷酶缺乏症猫的临床症状得到改善

期刊:Molecular Therapy
影响因子:12
doi:10.1038/mt.2015.168
Yoon, Sea Young; Bagel, Jessica H; O'Donnell, Patricia A; Vite, Charles H; Wolfe, John H
发表日期：2016
文献求助 收藏

Neonatal tolerance induction enables accurate evaluation of gene therapy for MPS I in a canine model

新生儿耐受诱导能够准确评估犬模型中MPS I的基因治疗效果

期刊:Molecular Genetics and Metabolism
影响因子:3.5
doi:10.1016/j.ymgme.2016.06.006
Hinderer, Christian; Bell, Peter; Louboutin, Jean-Pierre; Katz, Nathan; Zhu, Yanqing; Lin, Gloria; Choa, Ruth; Bagel, Jessica; O'Donnell, Patricia; Fitzgerald, Caitlin A; Langan, Therese; Wang, Ping; Casal, Margret L; Haskins, Mark E; Wilson, James M
基因治疗
发表日期：2016
文献求助 收藏

Neonatal Systemic AAV Induces Tolerance to CNS Gene Therapy in MPS I Dogs and Nonhuman Primates

新生儿全身性AAV诱导MPS I型犬和非人灵长类动物对中枢神经系统基因治疗产生耐受性

期刊:Molecular Therapy
影响因子:12
doi:10.1038/mt.2015.99
Hinderer, Christian; Bell, Peter; Louboutin, Jean-Pierre; Zhu, Yanqing; Yu, Hongwei; Lin, Gloria; Choa, Ruth; Gurda, Brittney L; Bagel, Jessica; O'Donnell, Patricia; Sikora, Tracey; Ruane, Therese; Wang, Ping; Tarantal, Alice F; Casal, Margret L; Haskins, Mark E; Wilson, James M
基因治疗
Primate
神经科学
发表日期：2015
文献求助 收藏

Intrathecal gene therapy corrects CNS pathology in a feline model of mucopolysaccharidosis I

鞘内基因疗法可纠正猫粘多糖贮积症 I 型模型中的中枢神经系统病理

期刊:Molecular Therapy
影响因子:12
doi:10.1038/mt.2014.135
Hinderer, Christian; Bell, Peter; Gurda, Brittney L; Wang, Qiang; Louboutin, Jean-Pierre; Zhu, Yanqing; Bagel, Jessica; O'Donnell, Patricia; Sikora, Tracey; Ruane, Therese; Wang, Ping; Haskins, Mark E; Wilson, James M
神经科学
发表日期：2014
文献求助 收藏

Cholesterol homeostatic responses provide biomarkers for monitoring treatment for the neurodegenerative disease Niemann-Pick C1 (NPC1)

胆固醇稳态反应可为监测神经退行性疾病尼曼-匹克C1型（NPC1）的治疗提供生物标志物

期刊:Human Molecular Genetics
影响因子:3.2
doi:10.1093/hmg/ddu331
Tortelli, Brett; Fujiwara, Hideji; Bagel, Jessica H; Zhang, Jessie; Sidhu, Rohini; Jiang, Xuntian; Yanjanin, Nicole M; Shankar, Roopa Kanakatti; Carillo-Carasco, Nuria; Heiss, John; Ottinger, Elizabeth; Porter, Forbes D; Schaffer, Jean E; Vite, Charles H; Ory, Daniel S
NPC1
神经科学
代谢
发表日期：2014
文献求助 收藏

Electrodiagnostic testing and histopathologic changes confirm peripheral nervous system myelin abnormalities in the feline model of niemann-pick disease type C

电诊断测试和组织病理学变化证实了猫尼曼-匹克病C型模型存在周围神经系统髓鞘异常。

期刊:Journal of Neuropathology and Experimental Neurology
影响因子:3
doi:10.1097/NEN.0b013e318286587f
Bagel, Jessica H; Sikora, Tracey U; Prociuk, Maria; Pesayco, Jill P; Mizisin, Andrew P; Shelton, G Diane; Vite, Charles H
神经科学
发表日期：2013
文献求助 收藏