Use of polyadenosine tail mimetics to enhance mRNA expression from genes associated with haploinsufficiency disorders
使用多聚腺苷酸尾模拟物来增强与单倍体不足疾病相关的基因的 mRNA 表达
期刊:Molecular Therapy-Nucleic Acids
影响因子:6.5
doi:10.1016/j.omtn.2025.102453
Bahareh Torkzaban, Yining Zhu, Christian Lopez, Jonathan M Alexander, Jingyao Ma, Yongzhi Sun, Katharine R Maschhoff, Wenqian Hu, Michele H Jacob, Dingchang Lin, Hai-Quan Mao, Sophie Martin, Jeff Coller