日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Engineered microRNA scaffolds for potent gene silencing in vivo.

工程化microRNA支架用于体内强效基因沉默

Militello Giuseppe, Greig Alyssa, Bi Chongfeng, Vasileva Ana, Zavodszky Maria I, Lo Shih-Ching, Guilmette Edward, Clarner Pete, Liu Bin, Bhat Guruharsha, Suh Junghae, Dow Lukas, Zuber Johannes, Fellmann Christof, Premsrirut Prem K

Inhibition of immune response reduces pathology in dorsal root ganglia and peripheral nerves in cynomolgus macaques following AAV gene therapy

抑制免疫反应可减轻食蟹猴在接受腺相关病毒(AAV)基因治疗后背根神经节和周围神经的病理变化。

Grubor, Branka; Henry, Kate L; Chan, Su Jing; Sheehan, Mark; Shah, Anumeha; Pellerin, Alex; Bai, Judy; Nadella, Prasad; Bommegowda, Santhosh; Cullen, Patrick; Tien, Eric; Chen, Vivian; van der Munnik, Nicholas P; White-Hunt, Stephanie; Plowey, Edward D; Hamann, Stefan; Guise, Amanda J; Xu, Shanqin; Kirkland, Melissa; Doherty, Jessica; Lyashenko, Eugenia; Bhat, Guruharsha; Glajch, Kelly; Lo, Shih-Ching; Gianni, Davide; Clarner, Pete; Gagnon, Jake; Chu, Jenhwa; Nambiar, Kalyani; Lulla, Mukesh; Zheng, Fengmei; Weldeab, Asmerom; Bartlett, Dan; Gutnick, Amos; Reynolds, Taylor; Zhu, Kan; Huh, Dann; Carlile, Thomas M; Fikes, James; Trapa, Patrick; Suh, Junghae; Morris, Dale; Burkly, Linda