日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Enhanced-mRNA Delivery Using Ultrasound-Delivered Anchors for Bioorthogonal Ligation

利用超声递送锚定物增强mRNA递送以进行生物正交连接

Di Ianni, Emilio; Jeon, Jueun; Mohammadi, Sedra; Hu, Huiyu; Quintana, Jeremy M; Lee, Chanseo; Haidar, Edwina Abou; Goemans, Marie; Zargani-Piccardi, Ayrton; Mahamdeh, Mohammed; Hernández, Iván Coto; Rodriguez, Victoria E; Zhou, Yirong; Aguirre, Aaron; Yuan, Shiaulou; Ng, Thomas S C; Breyne, Koen; Lee, Hakho; Breakefield, Xandra O; Miller, Miles A

Glioblastoma Cortical Organoids Recapitulate Cell-State Heterogeneity and Intercellular Transfer

胶质母细胞瘤皮质类器官重现细胞状态异质性和细胞间转移

Mangena, Vamsi; Chanoch-Myers, Rony; Sartore, Rafaela; Paulsen, Bruna; Gritsch, Simon; Weisman, Hannah; Hara, Toshiro; Breakefield, Xandra O; Breyne, Koen; Regev, Aviv; Chung, Kwanghun; Arlotta, Paola; Tirosh, Itay; Suvà, Mario L

Engineering of CD63 Enables Selective Extracellular Vesicle Cargo Loading and Enhanced Payload Delivery.

CD63 的工程改造可实现选择性细胞外囊泡货物装载和增强有效载荷递送

Obuchi Wataru, Zargani-Piccardi Ayrton, Leandro Kevin, Rufino-Ramos David, Di Lanni Emilio, Frederick Dawn Madison, Maalouf Katia, Nieland Lisa, Xiao Tianhe, Repiton Pierre, Vaine Christine A, Kleinstiver Benjamin P, Bragg D Cristopher, Lee Hakho, Miller Miles A, Breakefield Xandra O, Breyne Koen

CRISPR targeting of mmu-miR-21a through a single adeno-associated virus vector prolongs survival of glioblastoma-bearing mice

利用单个腺相关病毒载体进行 CRISPR 靶向 mmu-miR-21a 可延长胶质母细胞瘤小鼠的生存期。

Lisa Nieland ,Anne B Vrijmoet ,Isabelle W Jetten ,David Rufino-Ramos ,Alexandra J E M de Reus ,Koen Breyne ,Benjamin P Kleinstiver ,Casey A Maguire ,Marike L D Broekman ,Xandra O Breakefield ,Erik R Abels

Intratumoral delivery of 4-1BBL boosts IL-12-triggered anti-glioma immunity.

肿瘤内注射 4-1BBL 可增强 IL-12 触发的抗胶质瘤免疫力。

Lunavat Taral R, Nieland Lisa, van de Looij Sanne M, de Reus Alexandra J E M, Couturier Charles P, El Farran Chadi A, Miller Tyler E, Lill Julia K, Schübel Maryam, Xiao Tianhe, Di Ianni Emilio, Woods Elliot C, Sun Yi, Rufino-Ramos David, van Solinge Thomas S, Mahjoum Shadi, Grandell Emily, Li Mao, Mangena Vamsi, Dunn Gavin P, Jenkins Russell W, Mempel Thorsten R, Breakefield Xandra O, Breyne Koen

Intracellular and Extracellular Vesicle miRNA Signatures in Human iPSC-Derived Neural Stem Cells and Floor Plate Progenitors.

人类 iPSC 衍生的神经干细胞和底板祖细胞的细胞内和细胞外囊泡 miRNA 特征

Cruz Lilian, Ferreira Frederico Moraes, Lopes-Ramos Camila Miranda, Wei Zhiyun, Hendriks William T, Jinnah H A, Nakaya Helder I, Bragg D Cristopher, Krichevsky Anna M, Breakefield Xandra Owens, Hohmuth Lopes Marilene

Nucleic acid nanobiosystems for cancer theranostics: an overview of emerging trends and challenges

用于癌症诊疗一体化的核酸纳米生物系统:新兴趋势与挑战概述

Rebolledo, Laura P; Andrade, Luciana N S; Bajgelman, Marcio C; Banks, Lawrence; Breakefield, Xandra O; Dobrovolskaia, Marina A; Dokholyan, Nikolay V; Kimura, Edna T; Villa, Luisa; Zerbini, Luiz F; Zucolotto, Valtencir; Afonin, Kirill A; Strauss, Bryan E; Chammas, Roger; de Freitas Saito, Renata

Extracellular vesicles for the delivery of gene therapy

用于基因治疗递送的细胞外囊泡

Di Ianni, Emilio; Obuchi, Wataru; Breyne, Koen; Breakefield, Xandra O

AAV hamartin gene therapy in a stochastic, cerebral mouse model of tuberous sclerosis type 1

在随机性脑结节性硬化症1型小鼠模型中应用AAV hamartin基因疗法

Abou Haidar, Edwina; Prabhakar, Shilpa; Geffrey, Alexandra L; Mahamdeh, Mohammed; Tomeh, Tomeh; Breyne, Koen; Roumieh, Elie; Gurevich, Mia; Soberman, Roy J; Wojtkiewicz, Gregory R; Chen, John W; Han, Justin Seungkyu; Stemmer-Rachamimov, Anat; Breakefield, Xandra O

Exploring the potential of cell-derived vesicles for transient delivery of gene editing payloads

探索细胞来源囊泡在基因编辑有效载荷瞬时递送方面的潜力

Leandro, Kevin; Rufino-Ramos, David; Breyne, Koen; Di Ianni, Emilio; Lopes, Sara M; Jorge Nobre, Rui; Kleinstiver, Benjamin P; Perdigão, Pedro R L; Breakefield, Xandra O; Pereira de Almeida, Luís