Complement activation in a phase Ib study of fordadistrogene movaparvovec for Duchenne muscular dystrophy
在针对杜氏肌营养不良症的 fordadistrogene movaparvovec 的 Ib 期研究中,补体激活
期刊:Molecular Therapy
影响因子:12
doi:10.1016/j.ymthe.2025.06.032
Byrne, Barry J; Butterfield, Russell J; Shieh, Perry B; Smith, Edward C; Licht, Christoph; Binks, Michael; Casinghino, Sandra; Delnomdedieu, Marielle; Ravindra, Kodihalli C; McDonnell, Tara; Ryan, Kelly; Schulz, Martin; Shen, Qi; Shi, Heliang; Sirivelu, Madhu P; Vaidya, Vishal S; Whiteley, Laurence; Levy, Daniel I