日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Current clinical applications of AAV-mediated gene therapy

目前AAV介导的基因治疗的临床应用

Byrne, Barry J; Flanigan, Kevin M; Matesanz, Susan E; Finkel, Richard S; Waldrop, Megan A; D'Ambrosio, Eleonora S; Johnson, Nicholas E; Smith, Barbara K; Bönnemann, Carsten; Carrig, Sean; Rossano, Joseph W; Greenberg, Barry; Lalaguna, Laura; Lara-Pezzi, Enrique; Subramony, Sub; Corti, Manuela; Mercado-Rodriguez, Claudia; Leon-Astudillo, Carmen; Ahrens-Nicklas, Rebecca; Bharucha-Goebel, Diana; Gao, Guangping; Gessler, Dominic J; Hwu, Wuh-Liang; Chien, Yin-Hsiu; Lee, Ni-Chung; Boye, Sanford L; Boye, Shannon E; George, Lindsey A

Use of CD19-targeted immune modulation to eradicate AAV-neutralizing antibodies.

利用 CD19 靶向免疫调节来根除 AAV 中和抗体

Doshi Bhavya S, Markmann Caroline A, Novak Noelle, Juarez Rojas Silvia, Davidson Robert, Chau Julia Q, Wang Wei, Carrig Sean, Martos Rus Cristina, Samelson-Jones Benjamin J, Small Juliana C, Bhoj Vijay G, George Lindsey A