日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

A combinatorial synthetic strategy for developing genome-editing protein-delivery agents targeting mouse retina

一种用于开发靶向小鼠视网膜的基因组编辑蛋白递送载体的组合合成策略

Zhang, Jianye; Hołubowicz, Rafał; Smidak, Roman; Hu, Yulun; Du, Samuel W; Felgner, Jiin H; Palczewska, Grazyna; Rodrigues Menezes, Carolline; Risaliti, Eleonora; Dong, Zhiqian; Ma, Xiuli; Shayegan, Mojtaba H; Chen, Paul Z; Xing, Li; Hołubowicz, Maria; Li, Bowen; Liu, David R; Felgner, Philip L; Tochtrop, Gregory P; Palczewski, Krzysztof

Mechanistic machine learning enables interpretable and generalizable prediction of prime editing outcomes

机制机器学习能够对主要编辑结果进行可解释且可推广的预测。

Hsu, Alvin; Chen, Peter J; Li, Angus H; Hemez, Colin F; Gao, Xin D; Terrey, Markus; Nelson, Charlie; Selvam, Vijay; Cristian, Ana; McElroy, Amber N; Steinbeck, Benjamin J; Mahadeshwar, Gandhar K; Pandey, Smriti; Barsdale, Zachary; Chen, Paul Z; Sousa, Alexander A; Sakai, Holt A; Silverstein, Rachel A; Morad, Ilias; Krueger, Ryan K; Shen, Max W; Kleinstiver, Benjamin P; Lutz, Cathleen M; Tolar, Jakub; Blazar, Bruce R; Osborn, Mark J; Liu, David R

TIGER: A tdTomato in vivo genome-editing reporter mouse for investigating precision-editor delivery approaches

TIGER:一种用于研究精准编辑递送方法的tdTomato体内基因组编辑报告小鼠

Du, Samuel W; Palczewska, Grazyna; Dong, Zhiqian; Lauterborn, Julie C; Kaipa, Balasankara Reddy; Yan, Alexander L; Hołubowicz, Rafał; Ha, Siyoung; Chen, Paul Z; Gall, Christine M; Zode, Gulab; Liu, David R; Palczewski, Krzysztof

Scalable purification enables high-quality virus-like particles for therapeutic translation.

可扩展的纯化技术能够制备高质量的病毒样颗粒,用于治疗转化。

Hołubowicz Rafal, Gao Fangyuan, Du Samuel W, Rodrigues Menezes Carolline, Zhang Jianye, Hołubowicz Maria W, Chen Paul Z, Armbrust Niklas, Geilenkeuser Julian, Liu David R, Truong Dong-Jiunn Jeffery, Westmeyer Gil Gregor, Palczewska Grazyna, Palczewski Krzysztof

Directed evolution of engineered virus-like particles with improved production and transduction efficiencies.

定向进化工程病毒样颗粒,以提高其生产和转导效率

Raguram Aditya, An Meirui, Chen Paul Z, Liu David R

Understanding why superspreading drives the COVID-19 pandemic but not the H1N1 pandemic

了解为什么超级传播是导致新冠肺炎疫情大流行而非H1N1流感大流行的主要原因。

Chen, Paul Z; Koopmans, Marion; Fisman, David N; Gu, Frank X

SARS-CoV-2 shedding dynamics across the respiratory tract, sex, and disease severity for adult and pediatric COVID-19

SARS-CoV-2 在呼吸道、性别以及成人和儿童 COVID-19 疾病严重程度中的脱落动态

Chen, Paul Z; Bobrovitz, Niklas; Premji, Zahra A; Koopmans, Marion; Fisman, David N; Gu, Frank X