日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Gene augmentation therapy attenuates retinal degeneration in a knockout mouse model of Fam161a retinitis pigmentosa

基因增强疗法可减轻 Fam161a 视网膜色素变性基因敲除小鼠模型中的视网膜变性

Chen Matsevich, Prakadeeswari Gopalakrishnan, Ning Chang, Alexey Obolensky, Avigail Beryozkin, Manar Salameh, Corinne Kostic, Dror Sharon, Yvan Arsenijevic, Eyal Banin

Homozygous Knockout of Cep250 Leads to a Relatively Late-Onset Retinal Degeneration and Sensorineural Hearing Loss in Mice

Cep250 纯合敲除导致小鼠相对较晚发生视网膜变性和神经性听力损失

Alaa Abu-Diab, Prakadeeswari Gopalakrishnan, Chen Matsevich, Marije de Jong, Alexey Obolensky, Ayat Khalaileh, Manar Salameh, Ayala Ejzenberg, Menachem Gross, Eyal Banin, Dror Sharon, Samer Khateb

Retinal Structure and Function in a Knock-in Mouse Model for the FAM161A- p.Arg523∗ Human Nonsense Pathogenic Variant

FAM161A- p.Arg523∗ 人类无义致病变异的敲入小鼠模型中的视网膜结构和功能

Chen Matsevich, Prakadeeswari Gopalakrishnan, Alexey Obolensky, Eyal Banin, Dror Sharon, Avigail Beryozkin

A new mouse model for retinal degeneration due to Fam161a deficiency

Fam161a 缺乏导致视网膜变性的新小鼠模型

Avigail Beryozkin, Chen Matsevich, Alexey Obolensky, Corinne Kostic, Yvan Arsenijevic, Uwe Wolfrum, Eyal Banin, Dror Sharon