日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Determining the Minimally Effective Dose of a Clinical Candidate Adeno-Associated Virus Vector in a Mouse Model of Hemophilia A

在A型血友病小鼠模型中确定临床候选腺相关病毒载体的最小有效剂量

Greig, Jenny A; Smith, Melanie K; Nordin, Jayme M L; Goode, Tamara; Chroscinski, Edward A; Buza, Elizabeth L; Schmidt, Nicole; Kattenhorn, Lisa M; Wadsworth, Samuel; Wilson, James M

Determining the Minimally Effective Dose of a Clinical Candidate AAV Vector in a Mouse Model of Crigler-Najjar Syndrome

确定 Crigler-Najjar 综合征小鼠模型中临床候选 AAV 载体的最低有效剂量

Jenny A Greig, Jayme M L Nordin, Christine Draper, Deirdre McMenamin, Edward A Chroscinski, Peter Bell, John T Gray, Laura K Richman, James M Wilson

AAV8 Gene Therapy for Crigler-Najjar Syndrome in Macaques Elicited Transgene T Cell Responses That Are Resident to the Liver

AAV8 基因疗法治疗恒河猴 Crigler-Najjar 综合征引发驻留在肝脏的转基因 T 细胞反应

Jenny A Greig, Roberto Calcedo, Leticia Kuri-Cervantes, Jayme M L Nordin, Jessica Albrecht, Erin Bote, Tamara Goode, Edward A Chroscinski, Peter Bell, Laura K Richman, Michael R Betts, James M Wilson

Registered report: tumour vascularization via endothelial differentiation of glioblastoma stem-like cells

注册报告:胶质母细胞瘤干细胞样细胞内皮分化介导的肿瘤血管生成

Denise Chroscinski ,Darryl Sampey ,Nimet Maherali

Registered report: the CD47-signal regulated protein alpha (SIRPa) interaction is a therapeutic target for human solid tumors

注册报告:CD47-信号调节蛋白α(SIRPa)相互作用是人类实体肿瘤的治疗靶点

Denise Chroscinski, Nimet Maherali, Erin Griner; Reproducibility Project: Cancer Biology

Registered report: Melanoma genome sequencing reveals frequent PREX2 mutations

注册报告:黑色素瘤基因组测序揭示频繁的 PREX2 突变

Denise Chroscinski, Darryl Sampey, Alex Hewitt; Reproducibility Project: Cancer Biology

CNTO 530 increases expression of HbA and HbF in murine models of β-thalassemia and sickle cell anemia

CNTO 530 可增加 β-地中海贫血和镰状细胞贫血小鼠模型中 HbA 和 HbF 的表达

Makropoulos, Dorie A; Achuthanandam, Ram; Avery, Justin; Wilson, Krista; Brosnan, Kerry; Miller, Andrew; Nesspor, Thomas; Chroscinski, Denise; Walker, Mindi; Egenolf, Devon; Huang, ChiChi; Bugelski, Peter J