日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Randomized, blinded trial of weekend vs daily prednisone in Duchenne muscular dystrophy

一项随机、双盲试验比较了周末服用泼尼松与每日服用泼尼松治疗杜氏肌营养不良症的效果

Escolar, D M; Hache, L P; Clemens, P R; Cnaan, A; McDonald, C M; Viswanathan, V; Kornberg, A J; Bertorini, T E; Nevo, Y; Lotze, T; Pestronk, A; Ryan, M M; Monasterio, E; Day, J W; Zimmerman, A; Arrieta, A; Henricson, E; Mayhew, J; Florence, J; Hu, F; Connolly, A M

Inhibition of the IKK/NF-κB pathway by AAV gene transfer improves muscle regeneration in older mdx mice.

通过 AAV 基因转移抑制 IKK/NF-κB 通路可改善老年 mdx 小鼠的肌肉再生

Tang Y, Reay D P, Salay M N, Mi M Y, Clemens P R, Guttridge D C, Robbins P D, Huard J, Wang B

Systemic delivery of AAV8 in utero results in gene expression in diaphragm and limb muscle: treatment implications for muscle disorders

在子宫内系统性递送AAV8可导致膈肌和四肢肌肉中的基因表达:对肌肉疾病的治疗意义

Koppanati, B M; Li, J; Xiao, X; Clemens, P R

A new adenoviral vector: Replacement of all viral coding sequences with 28 kb of DNA independently expressing both full-length dystrophin and beta-galactosidase

一种新型腺病毒载体:用28 kb DNA替换所有病毒编码序列,该DNA可独立表达全长肌营养不良蛋白和β-半乳糖苷酶。

Kochanek, S; Clemens, P R; Mitani, K; Chen, H H; Chan, S; Caskey, C T