A first-in-human phase I/IIa gene transfer clinical trial for Duchenne muscular dystrophy using rAAVrh74.MCK. GALGT2
使用 rAAVrh74.MCK. GALGT2 进行针对杜氏肌营养不良症的首次人体 I/IIa 期基因转移临床试验
期刊:Molecular Therapy-Methods & Clinical Development
影响因子:
doi:10.1016/j.omtm.2022.08.009
Kevin M Flanigan, Tatyana A Vetter, Tabatha R Simmons, Megan Iammarino, Emma C Frair, Federica Rinaldi, Louis G Chicoine, Johan Harris, John P Cheatham, Sharon L Cheatham, Brian Boe, Megan A Waldrop, Deborah A Zygmunt, Davin Packer, Paul T Martin
