日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Nanohybridization as a Route to a Water-Friendly Therapeutic Tool for Rescuing Misfolded Proteins

纳米杂交技术作为一种制备水溶性治疗工具以拯救错误折叠蛋白的途径

Bortoluzzi, Mary; Cencini, Aura; Rutigliano, Lavinia; Rilievo, Graziano; Cecconello, Alessandro; Tonolo, Federica; Molinari, Simone; Sacchetto, Roberta; Carotti, Marcello; Sandonà, Dorianna; Martinello, Tiziana; Ugolotti, Juri; Fresch, Barbara; Litti, Lucio; Vianello, Fabio; Magro, Massimiliano

Repairing the defective folding of alpha-sarcoglycan is needed to promote myogenic cell engraftment in 3D artificial muscle models of LGMDR3.

修复α-肌聚糖的缺陷折叠是促进LGMDR3 3D人工肌肉模型中肌源性细胞移植所必需的。

Maghin Edoardo, Benetollo Alberto, Scano Martina, Caccin Paola, Carraro Eugenia, Piccoli Martina, Sandonà Dorianna

CFTR corrector C17 rescues defective SERCA1 in bovine pseudomyotonia: a potential therapy for Brody myopathy

CFTR 校正因子 C17 可挽救牛假性肌强直中缺陷的 SERCA1:一种治疗布罗迪肌病的潜在疗法

Akyürek, Eylem E; Jacinto, Joana Gonçalves Pontes; Iori, Silvia; Bianchini, Elisa; Bolcato, Marilena; Costa, Roberta; Giantin, Mery; Carotti, Marcello; Dacasto, Mauro; Cenacchi, Giovanna; Sandonà, Dorianna; Gentile, Arcangelo; Sacchetto, Roberta

Zebrafish as a Model Organism for Research in Rare Genetic Neuromuscular Diseases

斑马鱼作为罕见遗传性神经肌肉疾病研究的模式生物

Akyürek, Eylem Emek; Erba, Martina; Dalla Barba, Francesco; Sandonà, Dorianna; Sacchetto, Roberta

The Accordion Zebrafish tq206 Mutant in the Assessment of a Novel Pharmaceutical Approach to Brody Myopathy

在评估治疗布罗迪肌病的新型药物方法时,使用手风琴斑马鱼tq206突变体进行研究。

Akyürek, Eylem Emek; Greco, Francesca; Tesoriero, Chiara; Dalla Barba, Francesco; Carotti, Marcello; Gorni, Giulia; Sandonà, Dorianna; Vettori, Andrea; Sacchetto, Roberta

Fetal bovine serum contains biologically available ATP

胎牛血清含有生物可利用的 ATP

Valentina Vultaggio-Poma, Leticia Scussel Bergamin, Simonetta Falzoni, Mario Tarantini, Anna Lisa Giuliani, Dorianna Sandonà, Patrizia Polverino De Laureto, Francesco Di Virgilio

Efficacy of Cystic Fibrosis Transmembrane Regulator Corrector C17 in Beta-Sarcoglycanopathy-Assessment of Patient's Primary Myotubes

囊性纤维化跨膜调节剂校正剂 C17 在 β-肌聚糖病中的疗效 - 患者原发性肌管的评估

Martina Scano, Alberto Benetollo, Francesco Dalla Barba, Eylem Emek Akyurek, Marcello Carotti, Roberta Sacchetto, Dorianna Sandonà

Synthesis and Evaluation of Bithiazole Derivatives As Potential α-Sarcoglycan Correctors

双噻唑衍生物作为潜在 α-肌聚糖校正剂的合成与评价

Giovanni Ribaudo, Marcello Carotti, Alberto Ongaro, Erika Oselladore, Martina Scano, Giuseppe Zagotto, Dorianna Sandonà, Alessandra Gianoncelli

Modeling Sarcoglycanopathy in Danio rerio

斑马鱼的肌聚糖病建模

Francesco Dalla Barba, Michela Soardi, Leila Mouhib, Giovanni Risato, Eylem Emek Akyürek, Tyrone Lucon-Xiccato, Martina Scano, Alberto Benetollo, Roberta Sacchetto, Isabelle Richard, Francesco Argenton, Cristiano Bertolucci, Marcello Carotti, Dorianna Sandonà

Customized bioreactor enables the production of 3D diaphragmatic constructs influencing matrix remodeling and fibroblast overgrowth

定制生物反应器能够生产3D膈肌结构,从而影响基质重塑和成纤维细胞过度增殖。

Maghin, Edoardo; Carraro, Eugenia; Boso, Daniele; Dedja, Arben; Giagante, Mattia; Caccin, Paola; Barna, Raluca Ana-Maria; Bresolin, Silvia; Cani, Alice; Borile, Giulia; Sandrin, Deborah; Romanato, Filippo; Cecchinato, Francesca; Urciuolo, Anna; Sandonà, Dorianna; De Coppi, Paolo; Pavan, Piero G; Piccoli, Martina