日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Evaluation of One-Stage Assays for the Monitoring of Recombinant Human Factor IX Padua Activity After Etranacogene Dezaparvovec Gene Therapy

评估用于监测 Etranacogene Dezaparvovec 基因治疗后重组人凝血因子 IX Padua 活性的单阶段检测方法

Astermark, Jan; Miesbach, Wolfgang; Coppens, Michiel; Gielen, Sander; Twisk, Jaap; Dolmetsch, Ricardo; Verweij, Stephanie; Monahan, Paul E; Ewenstein, Bruce M; Nuthalapati, Silpa; Galante, Nick; Young, Guy

Sex-specific NLRP3 activation in neutrophils promotes neutrophil recruitment and NETosis in the murine model of diffuse alveolar hemorrhage

在弥漫性肺泡出血的小鼠模型中,中性粒细胞中性别特异性的NLRP3激活促进中性粒细胞募集和NETosis。

Pierre-André Jarrot ,Jiyoun Kim ,William Chan ,Lukas Heger ,Nicolas Schommer ,Pierre Cunin ,Camila M S Silva ,Stéphane Robert ,Peter A Nigrovic ,Bruce Ewenstein ,Denisa D Wagner

Risk of Intracranial Hemorrhage in Persons with Hemophilia A in the United States: Real-World Retrospective Cohort Study Using the ATHNdataset

美国A型血友病患者颅内出血风险:基于ATHN数据集的真实世界回顾性队列研究

Hu, Jianzhong; Chandler, Martin; Manuel, Christopher Matthew; Caicedo, Jorge; Denne, Michael; Ewenstein, Bruce; Mokdad, Ali G; Xing, Shan; Recht, Michael

Inhibition of protein arginine deiminase 4 prevents inflammation-mediated heart failure in arthritis

抑制蛋白质精氨酸脱亚胺酶 4 可预防关节炎中炎症介导的心力衰竭

Lukas A Heger ,Nicolas Schommer ,Shoichi Fukui ,Stijn Van Bruggen ,Casey E Sheehy ,Long Chu ,Sridharan Rajagopal ,Dhanalakshmi Sivanandhan ,Bruce Ewenstein ,Denisa D Wagner

Psychometric evaluation of a patient-reported outcomes instrument for congenital thrombotic thrombocytopenic purpura

先天性血栓性血小板减少性紫癜患者报告结局工具的心理测量学评价

Oladapo, Abiola; Ito, Diane; Rodriguez, Ana María; Philpott, Stephanie; Krupnick, Robert; Allen, Veleka; Hibbard, Christopher; Scully, Marie; Ewenstein, Bruce

Structure and Function of Recombinant versus Plasma-Derived von Willebrand Factor and Impact on Multimer Pharmacokinetics in von Willebrand Disease

重组血管性血友病因子与血浆来源血管性血友病因子的结构和功能及其对血管性血友病多聚体药代动力学的影响

Gritsch, Herbert; Schrenk, Gerald; Weinhappl, Nina; Mellgård, Björn; Ewenstein, Bruce; Turecek, Peter L

BAX 335 hemophilia B gene therapy clinical trial results: potential impact of CpG sequences on gene expression

BAX 335 B型血友病基因治疗临床试验结果:CpG序列对基因表达的潜在影响

Konkle, Barbara A; Walsh, Christopher E; Escobar, Miguel A; Josephson, Neil C; Young, Guy; von Drygalski, Annette; McPhee, Scott W J; Samulski, R Jude; Bilic, Ivan; de la Rosa, Maurus; Reipert, Birgit M; Rottensteiner, Hanspeter; Scheiflinger, Friedrich; Chapin, John C; Ewenstein, Bruce; Monahan, Paul E

Rurioctocog alfa pegol PK-guided prophylaxis in hemophilia A: results from the phase 3 PROPEL study

在A型血友病中,基于药代动力学指导的Rurioctocog alfa pegol预防性治疗:PROPEL 3期研究结果

Klamroth, Robert; Windyga, Jerzy; Radulescu, Vlad; Collins, Peter W; Stasyshyn, Oleksandra; Ibrahim, Hishamshah Mohd; Engl, Werner; Tangada, Srilatha D; Savage, William; Ewenstein, Bruce

Recombinant ADAMTS13 reduces abnormally up-regulated von Willebrand factor in plasma from patients with severe COVID-19

重组ADAMTS13可降低重症COVID-19患者血浆中异常上调的血管性血友病因子

Turecek, Peter L; Peck, Rachel C; Rangarajan, Savita; Reilly-Stitt, Christopher; Laffan, Michael A; Kazmi, Rashid; James, Izabela; Dushianthan, Ahilanandan; Schrenk, Gerald; Gritsch, Herbert; Ewenstein, Bruce M; Mellgard, Bjorn; Erdlenbruch, Wolfhard; Jain, Nisha; Binder, Nikolaus B; Mumford, Andrew D

Results of a randomized phase III/IV trial comparing intermittent bolus versus continuous infusion of antihaemophilic factor (recombinant) in adults with severe or moderately severe haemophilia A undergoing major orthopaedic surgery

一项随机III/IV期试验的结果比较了在接受大型骨科手术的重度或中度重度A型血友病成人患者中,间歇性推注与持续输注抗血友病因子(重组)的疗效。

Pabinger, Ingrid; Mamonov, Vasily; Windyga, Jerzy; Engl, Werner; Doralt, Jennifer; Tangada, Srilatha; Spotts, Gerald; Ewenstein, Bruce