The European Medicines Agency's review of elexacaftor/tezacaftor/ivacaftor: extending its use to all people with cystic fibrosis aged 2 years and older who do not have two class I CFTR variants
欧洲药品管理局对 elexacaftor/tezacaftor/ivacaftor 的审查:将其使用范围扩大到所有 2 岁及以上、不携带两个 I 类 CFTR 变异体的囊性纤维化患者。
期刊:European Respiratory Journal
影响因子:21
doi:10.1183/13993003.01506-2025
Drai, Catherine; van der Woude, Hanneke J; Lexmond, Anne J; van den Hoorn, Tineke; Mol, Peter G M; Leacy, Finbarr P; Przybyszewska, Agnieszka; Sepodes, Bruno; Castelnovo, Thomas